共 50 条
- [1] DEVELOPMENT OF GENE THERAPY FOR DUCHENNE MUSCULAR DYSTROPHY USING SYSTEMIC DELIVERY OF AAV VECTORS EXPRESSING TRUNCATED DYSTROPHINS [J]. JOURNAL OF GENE MEDICINE, 2009, 11 (09): : 835 - 835
- [4] Retroviral vectors for gene therapy of Duchenne muscular dystrophy [J]. Neurological Sciences, 2000, 21 : S925 - S927
- [8] COMBINATORIAL GENE THERAPY USING AAV VECTOR TECHNOLOGY TO TREAT DUCHENNE MUSCULAR DYSTROPHY [J]. JOURNAL OF GENE MEDICINE, 2013, 15 (8-9): : 325 - 326