BURDEN OF ILLNESS OF SPINAL MUSCULAR ATROPHY: AN UPDATE

被引:0
|
作者
Droege, M. [1 ]
Dabbous, O. [1 ]
Arjunji, R. [1 ]
Patel, A. [1 ]
Gauthier-Loiselle, M. [2 ]
Cloutier, M. [2 ]
Sproule, D. M. [1 ]
机构
[1] AveXis Inc, Bannockburn, IL USA
[2] Anal Grp, Montreal, PQ, Canada
关键词
D O I
暂无
中图分类号
F [经济];
学科分类号
02 ;
摘要
PND24
引用
收藏
页码:S626 / S626
页数:1
相关论文
共 50 条
  • [1] BURDEN OF ILLNESS OF SPINAL MUSCULAR ATROPHY: AN UPDATE
    Droege, M.
    Dabbous, O.
    Arjunji, R.
    Gauthier-Loiselle, M.
    Cloutier, M.
    Sproule, D. M.
    [J]. VALUE IN HEALTH, 2019, 22 : S339 - S339
  • [2] Burden of illness of spinal muscular atrophy type 1 (SMA1): an update
    Droege, M.
    Dabbous, O.
    Arjunji, R.
    Gauthier-Loiselle, M.
    Cloutier, M.
    Sproule, D.
    [J]. NEUROMUSCULAR DISORDERS, 2020, 30 : S70 - S70
  • [3] BURDEN OF DISEASE AND COST OF ILLNESS OF SPINAL MUSCULAR ATROPHY IN PORTUGAL
    Costa, J.
    Coelho, T.
    Moreno, T.
    Negrao, L.
    Ribeiro, J.
    Santos, M.
    Santos, M. O.
    Vieira, J. P.
    Pinheiro, E.
    Guerreiro, R.
    Miguel, Silva L.
    Borges, M.
    [J]. VALUE IN HEALTH, 2022, 25 (01) : S53 - S53
  • [4] Spinal Muscular Atrophy: An Update
    Chang, Tracy
    Gieron-Korthals, Maria
    [J]. FETAL AND PEDIATRIC PATHOLOGY, 2011, 30 (02) : 130 - 136
  • [5] Burden of illness of spinal muscular atrophy type 1 (SMA1)
    Droege, M.
    Dabbous, O.
    Arjunji, R.
    Seda, J.
    Gauthier-Loiselle, M.
    Cloutier, M.
    Sproule, D.
    [J]. NEUROMUSCULAR DISORDERS, 2019, 29 : S128 - S128
  • [6] Burden of Illness of Spinal Muscular Atrophy Type 1 (SMA1)
    Droege, M.
    Dabbous, O.
    Arjunji, R.
    Seda, J.
    Gauthier-Loiselle, M.
    Cloutier, M.
    Sproule, D.
    [J]. ANNALS OF NEUROLOGY, 2019, 86 : S122 - S122
  • [7] Burden of illness of spinal muscular atrophy type 1 (SMA1)
    Droege, M.
    Dabbous, O.
    Arjunji, R.
    Seda, J.
    Gauthier-Loiselle, M.
    Cloutier, M.
    Sproule, D. M.
    [J]. EUROPEAN JOURNAL OF NEUROLOGY, 2019, 26 : 826 - 826
  • [8] Spinal muscular atrophy: a global view on the burden of illness and clinical trial readiness
    Verhaart, I. E. C.
    Robertson, A.
    Jones, C. C.
    Cook, S. F.
    Lochmuller, H.
    [J]. NEUROMUSCULAR DISORDERS, 2017, 27 : S30 - S30
  • [9] Burden of illness of spinal muscular atrophy type 1 (SMA1)
    Droege, M.
    Dabbous, O.
    Arjunji, R.
    Seda, J.
    Gauthier-Loiselle, M.
    Cloutier, M.
    Sproule, D. M.
    [J]. JOURNAL OF THE NEUROLOGICAL SCIENCES, 2019, 405
  • [10] THE BURDEN OF SPINAL MUSCULAR ATROPHY IN RUSSIA
    Kolbin, A.
    Kurylev, A.
    Balykina, Y.
    Proskurin, M.
    Mishinova, S.
    [J]. VALUE IN HEALTH, 2020, 23 : S632 - S632