Base Editing for Therapeutic Induction of Fetal Hemoglobin in ß-Thalassemia

被引：1
|
作者：
Christakopoulos, Georgios E. [1 ]
Mayuranathan, Thiyagaraj [2 ]
Fernandez, Alfonso G. [2 ]
Mayberry, Kalin [2 ]
Yao, Yu [2 ]
Telange, Rahul [2 ]
Dudley, Michael [2 ]
Levine, Rachel [2 ]
Dempsey, Erin [2 ]
Liu, David R. [3 ,4 ,5 ]
Yen, Jonathan S. [2 ,6 ,7 ]
Weiss, Mitchell J. [2 ]
机构：
[1] St Jude Childrens Res Hosp, Dept Oncol, Memphis, TN USA
[2] St Jude Childrens Res Hosp, Dept Hematol, Memphis, TN USA
[3] Harvard Univ, Howard Hughes Med Inst, Cambridge, MA USA
[4] Harvard Univ, Dept Chem & Chem Biol, Cambridge, MA USA
[5] Broad Inst MIT & Harvard, Merkin Inst Transformat Technol Healthcare, Cambridge, MA USA
[6] St Jude Childrens Res Hosp, Therapeut Genome Engn, Dept Hematol, S, Memphis, TN USA
[7] Beam Therapeut, Cambridge, MA USA
来源：
BLOOD | 2022年 / 140卷
关键词：
D O I：
10.1182/blood-2022-169391
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：10660 / 10661
页数：2
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