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- [1] Safety and Toxicology of Ocular Gene Therapy with Recombinant AAV Vector rAAV.hCNGA3 in Nonhuman PrimatesHUMAN GENE THERAPY CLINICAL DEVELOPMENT, 2019, 30 (02) : 50 - 56Tobias, Peters论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Tubingen, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyPhilipp, Seitz Immanuel论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyStylianos, Michalakis论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilian Univ Munich, Ctr Integrated Prot Sci Munich, Dept Pharm, Ctr Drug Res, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyMartin, Biel论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilian Univ Munich, Ctr Integrated Prot Sci Munich, Dept Pharm, Ctr Drug Res, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBarbara, Wilhelm论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyFelix, Reichel论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyAlexander, Ochakovski Guy论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyEberhart, Zrenner论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Werner Reichardt Ctr Integrat Neurosci, Tubingen, Germany Univ Tubingen, Ctr Ophthalmol, Inst Ophthalm Res, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyMarius, Ueffing论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Inst Ophthalm Res, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBirgit, Korbmacher论文数: 0 引用数: 0 h-index: 0机构: Covance Preclin Serv GmbH, Munster, Germany Univ Eye Hosp Tubingen, Tubingen, GermanySven, Korte论文数: 0 引用数: 0 h-index: 0机构: Covance Preclin Serv GmbH, Munster, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyUlrich, Bartz-Schmidt Karl论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyDominik, Fischer Manuel论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBartz-Schmidt, Karl Ulrich论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBolz, Sylvia论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyFischer, Dominik论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyKohl, Susanne论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyKuehlewein, Laura论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyMuehlfriedel, Regine论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyNeubauer, Jonas论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyOchakovski, Alex论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyPaquet-Durand, Francois论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanySeeliger, Mathias论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanySothilingam, Vithiyanjali论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyUeffing, Marius论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyWeisschuh, Nicole论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyWissinger, Bernd论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyZhour, Ahmad论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyZobor, Ditta论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyZrenner, Eberhart论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBiel, Martin论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyMichalakis, Stylianos论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanySchoen, Christian论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyKahle, Nadine论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyPeters, Tobias论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyWilhelm, Barbara论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyTsang, Steven论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Ophthalmol, New York, NY 10027 USA Univ Eye Hosp Tubingen, Tubingen, GermanyGloeckner, Christian Johannes论文数: 0 引用数: 0 h-index: 0机构: Deutsch Zentrum Neurodegenerat Erkrankungen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, Germany
- [2] Ocular Safety and Toxicology of Subretinal Gene Therapy With rAAV.hPDE6A in Nonhuman PrimatesTRANSLATIONAL VISION SCIENCE & TECHNOLOGY, 2025, 14 (01):Seitz, Immanuel P.论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, Germany Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanyWozar, Fabian论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, Germany Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanyOchakovski, Guy Alex论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Munich, Munich, Germany Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanyReichel, Felix F.论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, Germany Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanyKorte, Sven论文数: 0 引用数: 0 h-index: 0机构: Labcorp Early Dev Serv GmbH, Munster, Germany Virscio Inc, New Haven, CT USA Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanyKorbmacher, Birgit论文数: 0 引用数: 0 h-index: 0机构: Labcorp Early Dev Serv GmbH, Munster, Germany Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanyWilhelm, Barbara论文数: 0 引用数: 0 h-index: 0机构: STZeyetrial, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanySuesskind, Daniela论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, Germany Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanyBartz-Schmidt, Karl-Ulrich论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, Germany Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanyFischer, M. Dominik论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, Germany Univ Oxford, Nuffield Dept Clin Neurosci, Oxford, England Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, GermanyPeters, Tobias论文数: 0 引用数: 0 h-index: 0机构: STZeyetrial, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Tubingen, Univ Eye Hosp Tuebingen, Ctr Ophthalmol, Tubingen, Germany
- [3] Ocular and systemic safety of a recombinant AAV8 vector for X-linked retinoschisis gene therapy: GLP studies in rabbits and Rs1-KO miceMOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2016, 3Marangoni, Dario论文数: 0 引用数: 0 h-index: 0机构: NIDCD, NIH, Bethesda, MD 20892 USA Univ Aquila, Dept Biotechnol & Appl Clin Sci, Laquila, Italy NIDCD, NIH, Bethesda, MD 20892 USABush, Ronald A.论文数: 0 引用数: 0 h-index: 0机构: NIDCD, NIH, Bethesda, MD 20892 USA NIDCD, NIH, Bethesda, MD 20892 USAZeng, Yong论文数: 0 引用数: 0 h-index: 0机构: NIDCD, NIH, Bethesda, MD 20892 USA NIDCD, NIH, Bethesda, MD 20892 USAWei, Lisa L.论文数: 0 引用数: 0 h-index: 0机构: NEI, NIH, Bethesda, MD 20892 USA NIDCD, NIH, Bethesda, MD 20892 USAZiccardi, Lucia论文数: 0 引用数: 0 h-index: 0机构: NIDCD, NIH, Bethesda, MD 20892 USA GB Bietti Fdn, IRCCS, Dept Neurophysiol Vis & Neurophthalmol, Rome, Italy NIDCD, NIH, Bethesda, MD 20892 USAVijayasarathy, Camasamudram论文数: 0 引用数: 0 h-index: 0机构: NIDCD, NIH, Bethesda, MD 20892 USA NIDCD, NIH, Bethesda, MD 20892 USABartoe, Joshua T.论文数: 0 引用数: 0 h-index: 0机构: MPI Res, Mattawan, MI USA NIDCD, NIH, Bethesda, MD 20892 USAPalyada, Kiran论文数: 0 引用数: 0 h-index: 0机构: MPI Res, Mattawan, MI USA Merck Res Lab, Kenilworth, NJ USA NIDCD, NIH, Bethesda, MD 20892 USASantos, Maria论文数: 0 引用数: 0 h-index: 0机构: NIDCD, NIH, Bethesda, MD 20892 USA NIDCD, NIH, Bethesda, MD 20892 USAHiriyanna, Suja论文数: 0 引用数: 0 h-index: 0机构: NEI, NIH, Bethesda, MD 20892 USA NIDCD, NIH, Bethesda, MD 20892 USAWu, Zhijian论文数: 0 引用数: 0 h-index: 0机构: NEI, NIH, Bethesda, MD 20892 USA NIDCD, NIH, Bethesda, MD 20892 USAColosi, Peter论文数: 0 引用数: 0 h-index: 0机构: NEI, NIH, Bethesda, MD 20892 USA BioMarin Pharmaceut Inc, Novato, CA USA NIDCD, NIH, Bethesda, MD 20892 USASieving, Paul A.论文数: 0 引用数: 0 h-index: 0机构: NIDCD, NIH, Bethesda, MD 20892 USA NEI, NIH, Bethesda, MD 20892 USA NIDCD, NIH, Bethesda, MD 20892 USA
- [4] Assessment of toxicity and biodistribution of recombinant AAV8 vector-mediated immunomodulatory gene therapy in mice with Pompe disease (vol 1, pg 14018, 2014)MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2019, 13 : 493 - 493Wang, Gensheng论文数: 0 引用数: 0 h-index: 0Young, Sarah P.论文数: 0 引用数: 0 h-index: 0Bali, Deeksha论文数: 0 引用数: 0 h-index: 0Hutt, Julie论文数: 0 引用数: 0 h-index: 0Li, Songtao论文数: 0 引用数: 0 h-index: 0Benson, Janet论文数: 0 引用数: 0 h-index: 0Koeberl, Dwight D.论文数: 0 引用数: 0 h-index: 0
- [5] Intracerebral Gene Therapy Using AAVrh.10-hARSA Recombinant Vector to Treat Patients with Early-Onset Forms of Metachromatic Leukodystrophy: Preclinical Feasibility and Safety Assessments in Nonhuman PrimatesHUMAN GENE THERAPY CLINICAL DEVELOPMENT, 2015, 26 (02) : 113 - 124Zerah, Michel论文数: 0 引用数: 0 h-index: 0机构: INSERM, U986, F-94275 Le Kremlin Bicetre, France Necker Childrens Hosp, Pediat Neurosurg, F-75014 Paris, France INSERM, U986, F-94275 Le Kremlin Bicetre, FrancePiguet, Francoise论文数: 0 引用数: 0 h-index: 0机构: INSERM, U986, F-94275 Le Kremlin Bicetre, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceColle, Marie-Anne论文数: 0 引用数: 0 h-index: 0机构: INRA, U703, UMR, F-44000 Nantes, France Nantes Atlantic Coll Vet Med, Food Sci & Engn Oniris, F-44000 Nantes, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceRaoul, Sylvie论文数: 0 引用数: 0 h-index: 0机构: CHU Nord, Serv Neurochirurg, F-44000 Nantes, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceDeschamps, Jack-Yves论文数: 0 引用数: 0 h-index: 0机构: INRA, U703, UMR, F-44000 Nantes, France Nantes Atlantic Coll Vet Med, Food Sci & Engn Oniris, F-44000 Nantes, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceDeniaud, Johan论文数: 0 引用数: 0 h-index: 0机构: INRA, U703, UMR, F-44000 Nantes, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceGautier, Benoit论文数: 0 引用数: 0 h-index: 0机构: INSERM, U986, F-94275 Le Kremlin Bicetre, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceToulgoat, Frederique论文数: 0 引用数: 0 h-index: 0机构: CHU Nantes, Hop Laennec, Neuroradiol Diagnost & Intervent, F-44000 Nantes, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceBieche, Ivan论文数: 0 引用数: 0 h-index: 0机构: Fac Sci Pharmaceut & Biol Paris, F-75005 Paris, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceLaurendeau, Ingrid论文数: 0 引用数: 0 h-index: 0机构: Fac Sci Pharmaceut & Biol Paris, F-75005 Paris, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceSondhi, Dolan论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, New York, NY 10065 USA INSERM, U986, F-94275 Le Kremlin Bicetre, FranceSouweidane, Mark M.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Neurol Surg & Pediat, New York, NY 10065 USA INSERM, U986, F-94275 Le Kremlin Bicetre, FranceCartier-Lacave, Nathalie论文数: 0 引用数: 0 h-index: 0机构: INSERM, U986, F-94275 Le Kremlin Bicetre, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceMoullier, Philippe论文数: 0 引用数: 0 h-index: 0机构: INSERM, Atlantic Gene Therapies, UMR 1089, F-44000 Nantes, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceCrystal, Ronald G.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, New York, NY 10065 USA INSERM, U986, F-94275 Le Kremlin Bicetre, FranceRoujeau, Thomas论文数: 0 引用数: 0 h-index: 0机构: Hop Montpellier, Neurosurg, F-34000 Montpellier, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceSevin, Caroline论文数: 0 引用数: 0 h-index: 0机构: INSERM, U986, F-94275 Le Kremlin Bicetre, France Hop Bicetre, Neuropediat Unit, F-94275 Le Kremlin Bicetre, France INSERM, U986, F-94275 Le Kremlin Bicetre, FranceAubourg, Patrick论文数: 0 引用数: 0 h-index: 0机构: INSERM, U986, F-94275 Le Kremlin Bicetre, France Hop Bicetre, Neuropediat Unit, F-94275 Le Kremlin Bicetre, France INSERM, U986, F-94275 Le Kremlin Bicetre, France
- [6] Corneal fibrosis abrogation by a localized AAV-mediated inhibitor of differentiation 3 (Id3) gene therapy in rabbit eyes in vivo (vol 30, pg 3257, 2022)MOLECULAR THERAPY, 2022, 30 (10) : 3334 - 3334Gupta, Suneel论文数: 0 引用数: 0 h-index: 0Fink, Michael K.论文数: 0 引用数: 0 h-index: 0Kempuraj, Duraisamy论文数: 0 引用数: 0 h-index: 0Sinha, Nishant R.论文数: 0 引用数: 0 h-index: 0Martin, Lynn M.论文数: 0 引用数: 0 h-index: 0Keele, Landon M.论文数: 0 引用数: 0 h-index: 0Sinha, Prashant R.论文数: 0 引用数: 0 h-index: 0Giuliano, Elizabeth A.论文数: 0 引用数: 0 h-index: 0Hesemann, Nathan P.论文数: 0 引用数: 0 h-index: 0Raikwar, Sudhanshu P.论文数: 0 引用数: 0 h-index: 0Chaurasia, Shyam S.论文数: 0 引用数: 0 h-index: 0Mohan, Rajiv R.论文数: 0 引用数: 0 h-index: 0
- [7] Relevance of NHP safety studies for ocular delivery of AAV-based gene therapy in humans: Example of GS010 (rAAV2/2-ND4) local tolerability, shedding and immunogenicity for the treatment of Leber Hereditary Optic Neuropathy (LHON), after intravitreal (IVT) injection in non-human primates (NHP) and in LHON patientsINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2015, 56 (07)Thomasson, Nitza论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceGaly, Anne论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceFitoussi, Serge论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceMeunier, Sandrine论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceUretsky, Scott论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceCombal, Jean-Philippe论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, France