Platelet-Targeted Expression of Human BDD-FVIII Reduces Bleeding in Canine Hemophilia

被引:0
|
作者
Du, Lily M. [1 ]
Nichols, Timothy C. [2 ]
Haberichter, Sandra L. [1 ]
Jacobi, Paula M. [1 ]
Jensen, Eric S. [1 ]
Fang, Juan [1 ]
Shi, Qizhen [1 ]
Montgomery, Robert R. [1 ]
Wilcox, David A. [1 ]
机构
[1] Med Coll Wisconsin, Dept Pediat, Milwaukee, WI 53226 USA
[2] Univ N Carolina, Francis Owen Blood Res Lab, Chapel Hill, NC USA
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:289 / 289
页数:1
相关论文
共 50 条
  • [1] The Severe Spontaneous Bleeding Phenotype in a Novel Hemophilia a Rat Model with an Inversion Mutation Is Rescued By Platelet-Targeted FVIII Expression
    Shi, Qizhen
    Mattson, Jeremy G.
    Fahs, Scot A.
    Montgomery, Robert R.
    BLOOD, 2018, 132
  • [2] Platelet-Targeted FVIII Gene Therapy Restores Hemostasis and Induces Immune Tolerance for Hemophilia A
    Cai, Yuanhua
    Shi, Qizhen
    FRONTIERS IN IMMUNOLOGY, 2020, 11
  • [3] Platelet-Targeted Gene Therapy for Hemophilia
    Shi, Qizhen
    MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2018, 9 : 100 - 108
  • [4] The Impact of GPIba on the Efficacy of Platelet-Targeted FVIII Gene Therapy in Hemophilia a with Pre-Existing Anti-FVIII Immunity
    Chen, Juan
    Schroeder, Jocelyn
    Luo, Xiaofeng
    Montgomery, Robert R.
    Shi, Qizhen
    BLOOD, 2015, 126 (23)
  • [5] The impact of GPIb on platelet-targeted FVIII gene therapy in hemophilia A mice with pre-existing anti-FVIII immunity
    Chen, Juan
    Schroeder, Jocelyn A.
    Luo, Xiaofeng
    Montgomery, Robert R.
    Shi, Qizhen
    JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2019, 17 (03) : 449 - 459
  • [6] Platelet-Targeted Expression of Coagulation Factor VIII (FVIII) Shows Efficacy for Using the Dog as a Large Animal Model for Gene Therapy of Hemophilia
    Wilcox, David A.
    Du, Lily M.
    Haberichter, Sandra L.
    Jacobi, Paula M.
    Fang, Juan
    Jensen, Eric S.
    Shi, Qizhen
    Montgomery, Robert R.
    BLOOD, 2008, 112 (11) : 1208 - 1208
  • [7] Platelet-Targeted Gene Therapy for Hemophilia A with Inhibitor History
    Eapen, Mary
    Malec, Lynn M.
    Armant, Myriam A.
    Johnson, Bryon D.
    Shi, Qizhen
    Xu, Huiqing
    Du, Lily M.
    Jerkins, James H.
    Duffy, Lisa J.
    Bushman, Frederic D.
    Lee, Carole
    Petrichenko, Angelina
    Hematti, Peiman
    Brazauskas, Ruta
    Jobe, Shawn M.
    Hari, Parameswaran N.
    Wilcox, David A.
    NEW ENGLAND JOURNAL OF MEDICINE, 2025, 392 (04): : 412 - 414
  • [8] Treatment of a Hemophilia B Mouse Model with Platelet-Targeted Expression of Factor IX Padua
    Li, Binbin
    Wu, Zhihan
    Xu, Wenjue
    Han, Wenwen
    Liu, Jiayu
    Wang, Dawei
    Zhang, Guowei
    HUMAN GENE THERAPY, 2021, 32 (9-10) : 506 - 516
  • [9] Platelet-targeted gene therapy induces immune tolerance in hemophilia and beyond
    Kumar, Saurabh
    Schroeder, Jocelyn A.
    Shi, Qizhen
    JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2024, 22 (01) : 23 - 34
  • [10] The severe spontaneous bleeding phenotype in a novel hemophilia A rat model is rescued by platelet FVIII expression
    Shi, Qizhen
    Mattson, Jeremy G.
    Fahs, Scot A.
    Geurts, Aron M.
    Weiler, Hartmut
    Montgomery, Robert R.
    BLOOD ADVANCES, 2020, 4 (01) : 55 - 65