Breakthrough to Bedside: Bringing Gene Therapy to Neuromuscular Diseases

被引：1
作者：
Wilson, James M.
Mendell, Jerry R. [1 ,2 ,3 ]
机构：
[1] Nationwide Childrens Hosp, Pediat Res, Columbus, OH USA
[2] Nationwide Childrens Hosp, Pediat & Neurol, Columbus, OH USA
[3] Ohio State Univ, Nationwide Childrens Hosp, Abigail Wexner Res Inst, Columbus, OH 43210 USA
来源：
HUMAN GENE THERAPY CLINICAL DEVELOPMENT | 2019年 / 30卷 / 03期
关键词：
D O I：
10.1089/humc.2019.29049.int
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：93 / 96
页数：4
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