Improved Lentiviral Vectors for the Cure of Hemoglobinopathies

被引:0
|
作者
Breda, Laura [1 ]
Ghiaccio, Valentina [1 ]
Zaidi, Hanyia [1 ]
Lourenco, Silvia Pires [1 ]
Casu, Carla [2 ]
Smith-Whitley, Kim [3 ]
Kwiatkowski, Janet L. [4 ]
Carrion, Vanessa [5 ]
Guzikowski, Virginia [5 ]
Kurita, Ryo [6 ]
Nakamura, Yukio [6 ]
Rivella, Stefano [1 ]
机构
[1] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
[2] Childrens Hosp Philadelphia CHOP, Philadelphia, PA USA
[3] Childrens Hosp Philadephia, Div Hematol, Colket Bldg,11th Floor, Philadelphia, PA USA
[4] Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA
[5] Childrens Hosp Philadelphia, Div Hematol, Thalassemia Ctr, Philadelphia, PA 19104 USA
[6] RIKEN BioResource Ctr, Cell Engn Div, Tsukuba, Ibaraki, Japan
关键词
D O I
10.1182/blood-2018-99-111319
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
3477
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页数:2
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