CFTR Modulators for the Treatment of Cystic Fibrosis

被引:8
|
作者
Hadida, Sabine [1 ]
Van Goor, Fredrick [1 ]
Grootenhuis, Peter D. J. [1 ]
机构
[1] Vertex Pharmaceut Inc, San Diego, CA 92121 USA
关键词
TRANSMEMBRANE CONDUCTANCE REGULATOR; BIOAVAILABLE COMPOUND; PRIMARY CULTURES; WILD-TYPE; CORRECTORS; DEFECT; GENE; TRAFFICKING; DELTA-F508; TRANSPORT;
D O I
10.1016/S0065-7743(10)45010-1
中图分类号
R914 [药物化学];
学科分类号
100701 ;
摘要
引用
收藏
页码:157 / 173
页数:17
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