Treatment with Selective Inhibitors of Nuclear Export (SINE) Compounds Attenuates Dystrophic Symptoms in Zebrafish and Mouse Models of Duchenne Muscular Dystrophy

被引：0
|
作者：
English, Katherine G. [1 ,2 ]
Samani, Adrienne [1 ,2 ]
Reid, Andrea L. [1 ,2 ]
Walker, Christopher J. [3 ]
Tamir, Sharon [3 ]
Alexander, Matthew S. [1 ,2 ,4 ,5 ,6 ]
机构：
[1] Childrens Alabama, Dept Pediat, Div Neurol, Birmingham, AL USA
[2] Univ Alabama Birmingham, Birmingham, AL USA
[3] Karyopharm Therapeut, Newton, MA USA
[4] Univ Alabama Birmingham, Dept Genet, Birmingham, AL USA
[5] UAB, Civitan Int Res Ctr CIRC, Birmingham, AL USA
[6] UAB, Ctr Neurodegenerat & Expt Therapeut CNET, Birmingham, AL USA
来源：
NEUROTHERAPEUTICS | 2022年 / 19卷 / 04期
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暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
32
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收藏
页码：1428 / 1429
页数：2
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