Lentiviral-Mediated Gene Therapy for the Treatment of Adenosine Deaminase 2 Deficiency

被引：0

作者：

Mortellaro, Alessandra ^{[1
]}

Zoccolillo, Matteo ^{[1
]}

Nunez, Cristina Mesa ^{[1
]}

Brix, Alessia ^{[2
]}

Brigida, Immacolata ^{[1
]}

Barzaghi, Federica ^{[3
]}

Scala, Serena ^{[1
]}

Hernandez, Raisa Jofra ^{[1
]}

Basso-Ricci, Luca ^{[1
]}

Colantuoni, Mariasilva ^{[1
,4
]}

Cesaro, Simone ^{[5
]}

Conti, Francesca ^{[6
]}

Pession, Andrea ^{[6
]}

Benedetti, Fabio ^{[7
]}

Gattorno, Marco ^{[8
]}

Naldini, Luigi ^{[1
,4
]}

Cicalese, Maria Pia

Pistocchi, Anna ^{[2
]}

Aiuti, Alessandro ^{[1
,3
,4
]}

机构：

[1] IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy

[2] Univ Studi Milano, Dept Med Biotechnol & Translat Med, Milan, Italy

[3] IRCCS San Raffaele Sci Inst, Pediat Immunohematol & Bone Marrow Transplantat U, Milan, Italy

[4] Univ Vita Salute San Raffaele, Milan, Italy

[5] Osped Donna & Bambino, Pediat Hematol Oncol, Verona, Italy

[6] IRCCS Azienda Osped Univ Bologna, Pediat Unit, Bologna, Italy

[7] Azienda Osped Univ Verona, Hematol & Stem Cell Transplantat, Verona, Italy

[8] IRCCS Ist Giannina Gaslini, Ctr Malattie Autoinfiammatorie & Immunodeficienz, Genoa, Italy

来源：

BLOOD | 2021年 / 138卷

关键词：

D O I：

10.1182/blood-2021-152127

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页数：3

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[1] Lentiviral-mediated gene therapy for the treatment of adenosine deaminase 2 deficiency
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