Clinical Characteristics of Classic Paroxysmal Nocturnal Hemoglobinuria (PNH) in Pediatric Patients: A Comparison with Classic PNH in Adults. An International PNH Registry Study

被引:1
|
作者
Urbano-Ispizua, Alvaro [1 ]
Schrezenmeier, Hubert [2 ,3 ]
Muus, Petra [4 ]
Maciejewski, Jaroslaw P. [5 ]
Socié, Gerard [6 ]
Szer, Jeffrey [7 ]
Brodsky, Robert A. [8 ]
Bessler, Monica [9 ]
Rosse, Wendell F. [10 ]
Kanakura, Yuzuru [11 ]
Khursigara, Gus [12 ]
Bedrosian, Camille L. [12 ]
Hillmen, Peter [13 ]
机构
[1] Hosp Clin Barcelona, IDIBAPS, Barcelona, Spain
[2] Univ Hosp Ulm, Ulm, Germany
[3] German Red Cross Blood Transfus Serv Baden Wurtte, Ulm, Germany
[4] Radboud Univ Nijmegen, Med Ctr, Dept Hematol, NL-6525 ED Nijmegen, Netherlands
[5] Cleveland Clin, Taussig Canc Inst, Cleveland, OH 44106 USA
[6] St Louis Hosp, Paris, France
[7] Royal Melbourne Hosp, Clin Haematol & BMT Serv, Parkville, Vic 3050, Australia
[8] Johns Hopkins Univ, Dept Med, Div Hematol, Baltimore, MD USA
[9] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
[10] Duke Univ, Med Ctr, Durham, NC USA
[11] Osaka Univ, Grad Sch Med, Osaka, Japan
[12] Alexion Pharmaceut Inc, Global Clin Dev, Cheshire, CT USA
[13] St James Univ Hosp, Dept Haematol, Leeds, W Yorkshire, England
关键词
D O I
10.1182/blood.V118.21.2102.2102
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:921 / 921
页数:1
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