Real-world data in children with achondroplasia after licensing of Vosoritide

被引：0

作者：

Palm, Katja ^{[1
]}

Bechthold-Dalla Pozza, Susanne ^{[2
]}

Gausche, Ruth ^{[3
]}

Hoegler, Wolfgang ^{[4
]}

Hoyer-Kuhn, Heike ^{[5
,6
]}

Huebner, Angela ^{[7
]}

Keller, Alexandra ^{[8
]}

Mirante, Alice ^{[9
]}

Mohnike, Klaus ^{[1
,10
]}

Muschol, Nicole ^{[11
]}

Nader, Sean ^{[12
]}

Pfaeffle, Roland ^{[3
]}

Quitter, Friederike ^{[7
]}

Rohrer, Tilmann ^{[13
]}

Rutsch, Frank ^{[14
]}

Schnabel, Dirk ^{[15
]}

Semler, Oliver ^{[16
,17
]}

Silva, Isabel ^{[18
]}

Sousa, Sergio B. ^{[18
]}

Voelkl, Thomas M. K. ^{[19
]}

Wechsung, Katja ^{[15
]}

Weigel, Johannes

Woelffle, Joachim ^{[20
]}

Lausch, Ekkehart ^{[21
]}

机构：

[1] Dept Paediat, Magdeburg, Germany

[2] Ludwig Maximilians Univ Munchen, Childrens Hosp, Pediat Endocrinol, Munich, Germany

[3] Univ Leipzig, Childrens Hosp, Pediat Endocrinol, Leipzig, Germany

[4] Johannes Kepler Univ Linz, Dept Paediat, Linz, Austria

[5] Univ Cologne, Fac Med, Dept Pediat, Cologne, Germany

[6] Univ Hosp Cologne, Cologne, Germany

[7] Tech Univ Dresden, Univ Klinikum, Childrens Hosp, Pediat Endocrinol, Dresden, Germany

[8] Childrens Ctr Johannispl, Leipzig, Germany

[9] Ctr Hosp & Univ Coimbra, Paediat Endocrinol Diabet & Growth Unit, Hosp Pediat, Coimbra, Portugal

[10] Cent German Competence Network Rare Dis MKSE, Magdeburg, Germany

[11] Univ Med Ctr Hamburg Eppendorf, Int Ctr Lysosomal Storage Dis, Hamburg, Germany

[12] Schon Clin Vogtareuth, Paediat Orthopaed, Vogtareuth, Germany

[13] Saarland Univ Homburg, Childrens Hosp, Pediat Endocrinol, Homburg, Germany

[14] Univ Childrens Hosp, Munster, Germany

[15] Charite Univ Med Berlin, Ctr Chronically Sick Children, Pediat Endocrinol, Berlin, Germany

[16] Univ Cologne, Fac Med, Cologne, Germany

[17] Univ Hosp Cologne, Dept Pediat, Cologne, Germany

[18] Ctr Hosp & Univ Coimbra, Med Genet Unit, Hosp Pediat, Coimbra, Portugal

[19] Josefinum Augsburg, Childrens Hosp, Pediat Endocrinol, Augsburg, Germany

[20] Friedrich Alexander Univ Erlangen, Childrens Hosp, Erlangen, Germany

[21] Univ Freiburg, Childrens Hosp, Pediat Genet, Freiburg, Germany

来源：

HORMONE RESEARCH IN PAEDIATRICS | 2022年 / 95卷 / SUPPL 2期

关键词：

D O I：

暂无

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

P1-223

引用

页码：151 / 151

页数：1

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