First-In-Human Intrathecal Gene Transfer Study for Giant Axonal Neuropathy: Three-Year Study Review of Safety, Immunologic Responses and Interim Analysis of Efficacy

被引：0
|
作者：
Bharucha-Goebel, D.
Saade, D.
Jain, M.
Waite, M.
Norato, G.
Cheung, K.
Foley, A. R.
Soldatos, A.
Rybin, D.
Lehky, T.
Del Hoyo, Calcedo R.
Jacobson, S.
Samulski, R. J.
Gray, S.
Bonnemann, C.
机构：
来源：
ANNALS OF NEUROLOGY | 2019年 / 86卷
关键词：
Neuromuscular Disorders; Translational/Experimental Therapeutics; Genetics;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
260
引用
收藏
页码：S168 / S168
页数：1
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