HEALTH OUTCOME IMPROVEMENTS IN SPINAL MUSCULAR ATROPHY TYPE 1 PATIENTS WITH AVXS-101 GENE REPLACEMENT THERAPY

被引：0
|
作者：
Al-Zaidy, S. [1 ]
Pickard, A. S. [2 ]
Kotha, K. [3 ]
Alfano, L. [1 ]
Lowes, L. [1 ]
Paul, G. [3 ]
Church, K. [1 ]
Lehman, K. [3 ]
Sproule, D. M. [4 ]
Dabbous, O. [4 ]
Maru, B. [5 ]
Berry, K. [1 ]
Arnold, W. D. [1 ]
Kissel, J. T. [1 ]
Mendell, J. R. [1 ]
Shell, R. [1 ]
机构：
[1] Ohio State Univ, Columbus, OH 43210 USA
[2] Univ Illinois, Chicago, IL USA
[3] Nationwide Childrens Hosp, Columbus, OH USA
[4] AveXis Inc, Bannockburn, IL USA
[5] AveXis Inc, Rickmansworth, England
来源：
VALUE IN HEALTH | 2018年 / 21卷
关键词：
D O I：
10.1016/j.jval.2018.09.2593
中图分类号：
F [经济];
学科分类号：
02 ;
摘要：
PSY16
引用
收藏
页码：S438 / S438
页数：1
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