Mitapivat versus Placebo for Pyruvate Kinase Deficiency

被引：2
|
作者：
Shah, Ami J. [1 ]
Schwartz, Jonathan D. [2 ]
Segovia, Jose C. [3 ]
机构：
[1] Stanford Univ, Stanford, CA 94305 USA
[2] Rocket Pharmaceut, Cranbury, NJ 08512 USA
[3] Ctr Invest Energet Medioambient & Tecnol, Madrid, Spain
来源：
NEW ENGLAND JOURNAL OF MEDICINE | 2022年 / 386卷 / 26期
关键词：
D O I：
10.1056/NEJMc2206275
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：2538 / 2539
页数：3
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