Initial therapeutic response to enzyme replacement therapy with Myozyme® in a sibling cohort with late-onset Pompe disease

被引：0

作者：

Hughes, D. S. ^{[1
]}

Norwood, F. ^{[2
]}

Sawicka, E. ^{[3
]}

Milligan, A. ^{[1
]}

Pringle, S. ^{[1
]}

Bruce, R. ^{[1
]}

Goodwin, S. ^{[1
]}

Jennings, A. ^{[1
]}

Richfield, L. ^{[1
]}

Mehta, A. B. ^{[1
]}

机构：

[1] UCL Royal Free & Univ Coll Med Sch, Lysosomal Storage Disorders Unit, London WC1E 6BT, England

[2] Kings Coll Hosp London, Dept Neurol, London, England

[3] Princess Royal Univ Hosp, Dept Thorac Med, Kent, England

来源：

CLINICAL THERAPEUTICS | 2008年 / 30卷

关键词：

D O I：

暂无

中图分类号：

R9 [药学];

学科分类号：

1007 ;

摘要：

引用

页码：S29 / S30

页数：2

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