REAL-WORLD EVIDENCE RECOMMENDATIONS FOR GENE THERAPIES: REGULATORY VERSUS HEALTH TECHNOLOGY ASSESSMENT

被引:0
|
作者
Allen, G. [1 ]
Summers, D. M. [1 ]
Evans, J. [1 ]
机构
[1] Costello Med, Cambridge, England
关键词
D O I
暂无
中图分类号
F [经济];
学科分类号
02 ;
摘要
PBI43
引用
收藏
页码:S21 / S21
页数:1
相关论文
共 50 条
  • [1] REAL-WORLD EVIDENCE IN GENE THERAPIES: RECOMMENDATIONS VERSUS REALITY
    Allen, G.
    Warnants, E.
    Summers, D. M.
    Evans, J.
    VALUE IN HEALTH, 2019, 22 : S425 - S425
  • [2] COMMON THREADS: REGULATORY AND HEALTH TECHNOLOGY ASSESSMENT (HTA) AGENCIESAVTM RECOMMENDATIONS ON REAL-WORLD EVIDENCE (RWE) USE IN DECISION-MAKING
    Jaksa, A.
    Gatto, N.
    Case, A.
    VALUE IN HEALTH, 2020, 23 : S315 - S316
  • [3] UNDERSTANDING THE ROLE OF REAL-WORLD EVIDENCE IN HEALTH TECHNOLOGY ASSESSMENT FOR ORPHAN DRUGS
    Akesson, C.
    Llewellyn, S.
    Bagshaw, E.
    Kousoulakou, H.
    Larkin, M.
    VALUE IN HEALTH, 2019, 22 : S862 - S862
  • [4] HEALTH TECHNOLOGY PERFORMANCE ASSESSMENT: REAL-WORLD EVIDENCE FOR PUBLIC HEALTHCARE SUSTAINABILITY
    Guerra-Junior, Augusto Afonso
    Pires de Lemos, Livia Lovato
    Godman, Brian
    Bennie, Marion
    Serpa Osorio-de-Castro, Claudia Garcia
    Alvares, Juliana
    Heaney, Aine
    Vassallo, Carlos Alberto
    Wettermark, Bjorn
    Benguria-Arrate, Gaizka
    Gutierrez-Ibarluzea, Inaki
    Canuto Santos, Vania Cristina
    Petramale, Clarice Alegre
    Acurcio, Fransciso de Assis
    INTERNATIONAL JOURNAL OF TECHNOLOGY ASSESSMENT IN HEALTH CARE, 2017, 33 (02) : 279 - 287
  • [5] Real-world evidence: perspectives on challenges, value, and alignment of regulatory and national health technology assessment data collection requirements
    Sievers, Hannah
    Joos, Angelika
    Hiligsmann, Mickael
    INTERNATIONAL JOURNAL OF TECHNOLOGY ASSESSMENT IN HEALTH CARE, 2021, 37 (01)
  • [6] A REVIEW OF REAL-WORLD EVIDENCE IN HEALTH TECHNOLOGY ASSESSMENT DECISION- MAKING OF GENE THERAPIES IN THE US, CANADA, UK, EU4, AND JAPAN
    Dabbous, M.
    Gonzalez, Olid A.
    Raza, J.
    Waththuhewa, M.
    Griffiths, J.
    Dabbous, F.
    Sullivan, N.
    VALUE IN HEALTH, 2023, 26 (06) : S264 - S264
  • [7] Real-world data for efficient health technology assessment
    Hall, Peter S.
    EUROPEAN JOURNAL OF CANCER, 2017, 79 : 235 - 237
  • [8] Integration of real-world evidence from different data sources in health technology assessment
    Graili, Pooyeh
    Guertin, Jason R.
    Chan, Kelvin K. W.
    Tadrous, Mina
    JOURNAL OF PHARMACY AND PHARMACEUTICAL SCIENCES, 2023, 26 : 11460
  • [9] THE VALUE OF REAL-WORLD EVIDENCE (RWE) IN MELANOMA IN HEALTH TECHNOLOGY ASSESSMENT (HTA) APPRAISALS
    Shah, R.
    Gautam, R.
    Rai, M. K.
    Prasanna, R.
    VALUE IN HEALTH, 2022, 25 (12) : S317 - S317
  • [10] TARGETED LITERATURE REVIEW OF THE USE OF REAL-WORLD EVIDENCE FROM SINGLE REAL-WORLD DATA SOURCES AND IN META-ANALYSES: METHODOLOGIES AND RECOMMENDATIONS FROM HEALTH TECHNOLOGY ASSESSMENT BODIES
    Martin, C.
    Diawara, K.
    Jaiswal, A. K.
    Gamburg, R.
    Miller, J.
    Park, C.
    Ranjan, N.
    Mehta, A. M.
    Tamminina, D.
    Shah, T.
    Schmerold, L.
    Hood, D.
    VALUE IN HEALTH, 2024, 27 (06) : S14 - S15