ANTISENSE OLIGONUCLEOTIDE-MEDIATED UPREGULATION OF CFTR VIA STERIC BLOCK OF POST-TRANSCRIPTIONAL CONTROL ELEMENTS: A NOVEL APPROACH FOR CYSTIC FIBROSIS THERAPEUTICS
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作者:
Sasaki, S.
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Ionis Pharmaceut, Carlsbad, CA USAIonis Pharmaceut, Carlsbad, CA USA
Sasaki, S.
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Zhao, C.
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Ionis Pharmaceut, Carlsbad, CA USAIonis Pharmaceut, Carlsbad, CA USA
Zhao, C.
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Crosby, J.
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Ionis Pharmaceut, Carlsbad, CA USAIonis Pharmaceut, Carlsbad, CA USA
Crosby, J.
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Monia, B.
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Ionis Pharmaceut, Carlsbad, CA USAIonis Pharmaceut, Carlsbad, CA USA
Monia, B.
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Guo, S.
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Ionis Pharmaceut, Carlsbad, CA USAIonis Pharmaceut, Carlsbad, CA USA
机构:
Rosalind Franklin Univ Med & Sci, Ctr Genet Dis, Chicago Med Sch, N Chicago, IL 60064 USA
Rosalind Franklin Univ Med & Sci, Sch Grad & Postdoctoral Studies, N Chicago, IL 60064 USARosalind Franklin Univ Med & Sci, Ctr Genet Dis, Chicago Med Sch, N Chicago, IL 60064 USA
Michaels, Wren E.
Bridges, Robert J.
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Rosalind Franklin Univ Med & Sci, Ctr Genet Dis, Chicago Med Sch, N Chicago, IL 60064 USARosalind Franklin Univ Med & Sci, Ctr Genet Dis, Chicago Med Sch, N Chicago, IL 60064 USA