ANTISENSE OLIGONUCLEOTIDE-MEDIATED UPREGULATION OF CFTR VIA STERIC BLOCK OF POST-TRANSCRIPTIONAL CONTROL ELEMENTS: A NOVEL APPROACH FOR CYSTIC FIBROSIS THERAPEUTICS

被引:0
|
作者
Sasaki, S. [1 ]
Zhao, C. [1 ]
Crosby, J. [1 ]
Monia, B. [1 ]
Guo, S. [1 ]
机构
[1] Ionis Pharmaceut, Carlsbad, CA USA
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D O I
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中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
9
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页码:S216 / S217
页数:2
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