One-year Outcomes Following Treatment with Nusinersen: Interim Results from the NURTURE Study of Presymptomatic Infants with Genetically Diagnosed Spinal Muscular Atrophy (SMA)

被引：0
|
作者：
De Vivo, D.
Bertini, E.
Hwu, W-L
Foster, R.
Gheuens, S.
Farwell, W.
Reyna, S.
机构：
来源：
ANNALS OF NEUROLOGY | 2017年 / 82卷
关键词：
Translational Therapeutics; Neonatal Neurology; Neuromuscular Disorders;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
PL2-4
引用
收藏
页码：S265 / S266
页数：2
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    [J]. NEUROMUSCULAR DISORDERS, 2017, 27 : S212 - S212
  • [2] Nusinersen in infants who initiate treatment in a presymptomatic stage of spinal muscular atrophy (SMA): Interim results from the phase 2 nurture study
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    Swoboda, K. J.
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    Kirschner, J.
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    [J]. JOURNAL OF THE NEUROLOGICAL SCIENCES, 2019, 405
  • [3] Nusinersen in Infants Who Initiate Treatment in a Presymptomatic Stage of Spinal Muscular Atrophy (SMA): Interim Results From the Phase 2 NURTURE Study
    Finkel, Richard S.
    De Vivo, Darryl C.
    Swoboda, Kathryn J.
    Bertini, Enrico
    Hwu, Wuh-Liang
    Foster, Richard
    Bhan, Ishir
    Fradette, Stephanie
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    [J]. NEUROLOGY, 2020, 94 (15)
  • [4] Nusinersen in infants who initiate treatment in a presymptomatic stage of Spinal Muscular Atrophy (SMA): interim results from the phase 2 NURTURE study
    Sansone, V. A.
    De Vivo, D. C.
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    Hwu, W. -L.
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    Butterfield, R. J.
    Topaloglu, H.
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    Jong, Y. -J.
    Shu, F.
    Bevernage, S. P.
    Johnson, K.
    Foster, R.
    Bhan, I.
    Fradette, S.
    Farwell, W.
    [J]. EUROPEAN JOURNAL OF NEUROLOGY, 2019, 26 : 83 - 83
  • [5] Nusinersen in Infants Who Initiatte Treatment in a Presymptomatic Stage of Spinal Muscular Atrophy (SMA): Interim Efficacy and Safety Results From the Phase 2 NURTURE Study
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    Foster, Richard
    Bhan, Ishir
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    [J]. NEUROLOGY, 2019, 92 (15)
  • [6] Nusinersen in Infants Who Initiate Treatment in a Presymptomatic Stage of Spinal Muscular Atrophy (SMA): Interim Efficacy and Safety Results From the Phase 2 NURTURE Study
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    Hwu, W. L.
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    [J]. ANNALS OF NEUROLOGY, 2018, 84 : S392 - S392
  • [7] Nusinersen in infants who initiate treatment in a presymptomatic stage of spinal muscular atrophy: interim results from the phase 2 NURTURE study
    Ryan, M.
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    Sansone, V.
    Jong, Y.
    Shu, F.
    Foster, R.
    Bhan, I.
    Fradette, S.
    Farwell, W.
    [J]. NEUROMUSCULAR DISORDERS, 2019, 29 : S185 - S185
  • [8] Nusinersen in Infants who Initiate Treatment in a Presymptomatic Stage of Spinal Muscular Atrophy: Interim Results from the Phase 2 NURTURE Study
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    Jong, Y-J
    Shu, F.
    Johnson, K.
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    [J]. ANNALS OF NEUROLOGY, 2019, 86 : S117 - S117
  • [9] Interim Efficacy and Safety Results from the Phase 2 NURTURE Study Evaluating Nusinersen in Presymptomatic Infants with Spinal Muscular Atrophy
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    [J]. NEUROLOGY, 2017, 88
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    [J]. EUROPEAN JOURNAL OF NEUROLOGY, 2020, 27 : 9 - 9
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