Long-Term Safety and Efficacy of Voxelotor for Patients with Sickle Cell Disease: Results from an Open-Label Extension of the Phase 3 HOPE Trial

被引：2
|
作者：
Achebe, Maureen [1 ]
Hassab, Hoda [2 ,3 ]
Alkindi, Salam [4 ]
Brown, R. Clark Clark [5 ]
Telfer, Paul [6 ]
Biemond, Bart J. [7 ]
Gordeuk, Victor R. [8 ]
Lipato, Thokozeni [9 ]
Tonda, Margaret [10 ]
Gray, Sarah [10 ]
Howard, Joanna [11 ,12 ]
机构：
[1] Brigham & Womens, Div Hematol, Boston, MA USA
[2] Alexandria Univ, Paediat Dept, Alexandria, Egypt
[3] Alexandria Univ, Clin Res Ctr, Fac Med, Alexandria, Egypt
[4] Sultan Qaboos Univ, Coll Med, Muscat, Oman
[5] Atlanta AFLAC Canc Ctr 26 Blood Disorders Svc, Childrens Healthcare Atlanta, Dept Pediat, Atlanta, GA USA
[6] Queen Mary Univ London, Blizard Inst, London, England
[7] Acad Med Ctr, Dept Hematol, Amsterdam, Netherlands
[8] Univ Illinois, Div Hematol & Oncol, Dept Med, Sickle Cell Ctr, Chicago, IL USA
[9] Virginia Commonwealth Univ, Richmond, VA USA
[10] Global Blood Therapeut, San Francisco, CA USA
[11] Guys & St Thomas NHS Fdn Trust, London, England
[12] Kings Coll London, London, England
来源：
BLOOD | 2021年 / 138卷
关键词：
D O I：
10.1182/blood-2021-153582
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
3114
引用
收藏
页数：5
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