Allogeneic Hematopoietic Stem Cell Transplantation in Children and Adults with Chronic Granulomatous Disease (CGD): A Study of the Inborn Errors Working Party (IEWP) of the EBMT

被引：3

作者：

Chiesa, Robert ^{[1
]}

Wang, Junfeng ^{[2
,3
]}

Blok, Henric-Jan ^{[3
,4
]}

Neven, Benedicte ^{[5
]}

Moshous, Despina ^{[5
]}

Schulz, Ansgar ^{[6
]}

Hoenig, Manfred ^{[7
]}

Albert, Michael H. ^{[8
]}

Hauck, Fabian ^{[9
]}

Al-Seraihy, Amal ^{[10
,11
]}

Gozdzik, Jolanta ^{[12
]}

Ljungman, Per ^{[13
,14
,15
]}

Lindemans, Caroline A. ^{[16
]}

Kalwak, Krzysztof ^{[17
]}

Strahm, Brigitte ^{[18
]}

Schanz, Urs ^{[19
]}

Sedlacek, Petr ^{[20
]}

Sykora, Karl-Walter ^{[21
]}

Aksoylar, Serap ^{[22
]}

Locatelli, Franco ^{[23
]}

Stepensky, Polina ^{[24
]}

Wynn, Robert ^{[25
]}

Lum, Su Han ^{[26
]}

Zecca, Marco ^{[27
]}

Veys, Paul ^{[1
]}

Gennery, Andrew ^{[28
]}

Felber, Matthias ^{[29
]}

Lankester, Arjan ^{[3
]}

Guengoer, Tayfun ^{[30
]}

Slatter, Mary ^{[28
]}

机构：

[1] Great Ormond St Hosp NHS Trust, Bone Marrow Transplantat Dept, London, England

[2] EBMT Stat Unit, Leiden, Netherlands

[3] Leiden Univ, Med Ctr, Leiden, Netherlands

[4] EBMT Data Off Leiden, Leiden, Netherlands

[5] Necker Childrens Hosp, Assistance Publ Hop Paris, Paris, France

[6] Univ Med Ctr, Dept Pediat, Ulm, Germany

[7] Univ Med Ctr Ulm, Pediat, Ulm, Germany

[8] Ludwig Maximilians Univ Munchen, Dr von Hauner Univ Childrens Hosp, Munich, Germany

[9] Ludwig Maximilians Univ Munchen, Hauner Univ Childrens Hosp, Munich, Germany

[10] King Faisal Specialist Hosp & Res Ctr, Riyadh, Saudi Arabia

[11] King Faisal Specialist Hosp & Res Ctr, Paediat SCT Program, Riyadh, Saudi Arabia

[12] Jagiellonian Univ, Krakow, Poland

[13] Karolinska Univ Hosp, Dept Hematol & Cellular Therapy, Stockholm, Sweden

[14] Karolinska Univ Hosp, Dept Allogene Stem Cell Transplantat, Stockholm, Sweden

[15] Karolinska Inst, Stockholm, Sweden

[16] Wilhelmina Childrens Hosp, Pediat Blood & Bone Marrow Transplantat Program, Utrecht, Netherlands

[17] Med Univ, Wroclaw, Poland

[18] Univ Hosp Freiburg, Dept Pediat & Adolescent Med, Freiburg, Germany

[19] Univ Hosp Zurich, Dept Med Oncol & Hematol, Zurich, Switzerland

[20] Univ Hosp Motol, Dept Pediat Haematol & Oncol, Prague, Czech Republic

[21] Univ Childrens Hosp, Hannover, Germany

[22] Paediat BMT Ctr, Izmir, Turkey

[23] IRCCS Bambino Gesu Childrens Hosp, Dept Hematol Oncol & Cell & Gene Therapy, Rome, Italy

[24] Hadassah Univ Hosp, Dept Bone Marrow Transplantat, Jerusalem, Israel

[25] Royal Manchester Childrens Hosp, Dept Blood & Marrow Transplantat, Manchester, Lancs, England

[26] Newcastle Children Hosp, Pediat Bone Marrow Transplantat Dept, Newcastle, England

[27] Fdn IRCCS Policlin San Matteo, Pediat Hematol Oncol, Pavia, Italy

[28] Great North Childrens Hosp, Newcaslte, England

[29] Univ Zurich, Kinderspital Zurich, Zurich, Switzerland

[30] Univ Childrens Hosp, Zurich, Switzerland

来源：

BLOOD | 2018年 / 132卷

关键词：

D O I：

10.1182/blood-2018-99-114841

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

970

引用

页数：4

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