Successful late-stage disease treatment of P23H human RHO (hRHO) using ARCUS nuclease gene editing in a pig model of Autosomal Dominant Retinitis Pigmentosa (adRP)

被引：0
|
作者：
Jalligampala, Archana [1 ]
Noel, Jennifer M. [1 ]
Jacobs, Olivia Noelle [1 ]
Bradley, Alec Lynn [1 ]
Wang, Wei [1 ]
Jabbar, Maha Haleem [1 ]
Hasan, Nazarul [2 ]
Prestigiacomo, Joseph [1 ]
Smith, Jeff [3 ]
Bartsevich, Victor [3 ]
Viles, Kristi [3 ]
Jantz, Derek [3 ]
McCall, Maureen Ann [2 ]
机构：
[1] Univ Louisville, Ophthalmol & Visual Sci, Sch Med, Louisville, KY USA
[2] Univ Louisville, Anat Sci & Neurobiol, Sch Med, Louisville, KY USA
[3] Precis Biosci Inc, Durham, NC USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2022年 / 63卷 / 07期
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D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
1107
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页数：4
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