Duchenne muscular dystrophy: current cell therapies

被引：47
|
作者：
Sienkiewicz, Dorota [1 ]
Kulak, Wojciech [1 ]
Okurowska-Zawada, Bozena [1 ]
Paszko-Patej, Grazyna [1 ]
Kawnik, Katarzyna [1 ]
机构：
[1] Med Univ Bialystok, Dept Pediat Rehabil, PL-15274 Bialystok, Poland
来源：
THERAPEUTIC ADVANCES IN NEUROLOGICAL DISORDERS | 2015年 / 8卷 / 04期
关键词：
Duchenne muscular dystrophy; G-CSF; stem cells; COLONY-STIMULATING FACTOR; NEURAL STEM-CELLS; BONE-MARROW-CELLS; FACTOR G-CSF; SKELETAL-MUSCLE; NEURODEGENERATIVE DISEASES; MYOBLAST TRANSPLANTATION; GENE-THERAPY; IN-VIVO; RECOVERY;
D O I：
10.1177/1756285615586123
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
Duchenne muscular dystrophy is a genetically determined X-linked disease and the most common, progressive pediatric muscle disorder. For decades, research has been conducted to find an effective therapy. This review presents current therapeutic methods for Duchenne muscular dystrophy, based on scientific articles in English published mainly in the period 2000 to 2014. We used the PubMed database to identify and review the most important studies. An analysis of contemporary studies of stem cell therapy and the use of granulocyte colony-stimulating factor (G-CSF) in muscular dystrophy was performed.
引用
收藏
页码：166 / 177
页数：12
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