Enhanced factor VIII gene therapy for hemophilia a dogs with a novel Furin-evading factor VIII variant

被引:0
|
作者
Siner, J., I [1 ]
Samelson-Jones, B. [1 ]
Crudele, J. M. [2 ]
Zhou, S. [3 ]
Merricks, E. [4 ]
Nichols, T. [4 ]
Camire, R. M. [1 ]
Arruda, V. R. [1 ]
机构
[1] Childrens Hosp Philadelphia, Div Hematol, Pediat, Philadelphia, PA 19104 USA
[2] Univ Penn, Philadelphia, PA 19104 USA
[3] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
[4] Univ N Carolina, Pathol & Lab Med, Chapel Hill, NC USA
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R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
AS120
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页码:43 / 43
页数:1
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