Development of Therapeutic Strategies for SCN2A Mutation Related Disorders Using New In Vitro Modeling Techniques

被引：0
|
作者：
Rodriguez, Yacidzohara [1 ]
Dennys-Rivers, Cassandra [1 ]
Ray, Shrestha Sinha [1 ]
Roussel, Florence [1 ]
Rodrigo, Rochelle [1 ]
Lesman, Daniel [1 ]
Gaffney, Caleb [1 ]
Hartlaub, Annalisa [1 ]
Meyer, Kathrin [1 ,2 ]
Wein, Nicolas [1 ,2 ]
机构：
[1] Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA
[2] Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
来源：
MOLECULAR THERAPY | 2020年 / 28卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1119
引用
收藏
页码：484 / 484
页数：1
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