Characterization of the Retinal Phenotype in a Humanized FD Mouse Model with Defective ELP1 Splicing

被引：0
|
作者：
Chekuri, Anil [1 ,2 ,3 ,4 ,5 ]
Morini, Elisabetta [2 ,3 ,4 ,5 ]
Wang, Xia [1 ]
Logan, Emily [4 ,5 ]
Krauson, Aram [4 ,5 ]
Salani, Monica [4 ,5 ]
Dietrich, Paula [4 ,5 ]
Dragatsis, Loannis [6 ]
Vandenberghe, Luk [1 ]
Slaugenhaupt, Susan [4 ,5 ,7 ]
机构：
[1] Harvard Med Sch, Grousbeck Gene Therapy Ctr, Mass Eye & Ear, Boston, MA 02115 USA
[2] Broad Inst MIT & Harvard, Boston, MA USA
[3] Mass Gen Hosp, Neurol, Boston, MA USA
[4] Mass Gen Hosp, Ctr Genom Med, Res Inst, Boston, MA USA
[5] Harvard Med Sch, Boston, MA 02115 USA
[6] Univ Tennessee, Ctr Hlth Sci, Dept Physiol, Memphis, TN 38163 USA
[7] Mass Gen Hosp, Res Inst, Neurol, Boston, MA USA
来源：
MOLECULAR THERAPY | 2020年 / 28卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1124
引用
收藏
页码：486 / 486
页数：1
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