Impact of Inotersen on Functioning and Activities of Daily Living for Patients with Hereditary TTR Amyloidosis: Results from a Double-Blind Placebo-Controlled Trial

被引：0
|
作者：
Yarlas, Aaron [1 ]
Merlini, Giampaolo [2 ,3 ]
White, Michelle K. [1 ]
Kessler, Asia Sikora [1 ]
Lovley, Andrew [1 ]
Guthrie, Spencer D. [4 ]
Pollock, Michael [4 ]
Gertz, Morie A. [5 ]
机构：
[1] Optum, Johnston, RI USA
[2] Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Dept Mol Med, Pavia, Italy
[3] Univ Pavia, Pavia, Italy
[4] Akcea Therapeut, Cambridge, MA USA
[5] Mayo Clin, Div Hematol, Rochester, MN USA
来源：
BLOOD | 2018年 / 132卷
关键词：
D O I：
10.1182/blood-2018-99-119578
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
4812
引用
收藏
页数：2
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