CHARACTERISTICS OF PATIENTS WITH HEREDITARY TRANSTHYRETIN AMYLOIDOSIS-POLYNEUROPATHY (ATTRV PN) IN NEURO-TTRANSFORM, A PHASE 3 STUDY OF EPLONTERSEN

被引：0
|
作者：
Cruz, Marcia Waddington [1 ]
Barroso, Fabio [2 ]
Berk, John [3 ]
Chao, Chi-Chao [4 ]
Dasgupta, Noel [5 ]
Dyck, P. James B. [6 ]
Gertz, Morie [6 ]
Obici, Laura [7 ]
Parman, Yesim [8 ]
Weiler, Markus [9 ]
Wixner, Jonas [10 ]
Viney, Nicholas [11 ]
Jung, Shiangtung [11 ]
Schneider, Eugene [11 ]
Coelho, Teresa [12 ]
机构：
[1] Fed Univ Rio Janei, Univ Hosp, Natl Amyloidosis Referral Ctr CEPARM, Rio De Janeiro, Brazil
[2] FLENI, Buenos Aires, DF, Argentina
[3] Boston Med Ctr, Boston, MA USA
[4] Natl Taiwan Univ Hosp, Taipei, Taiwan
[5] Indiana Univ Sch Med, Indianapolis, IN 46202 USA
[6] Mayo Clin, Rochester, MN USA
[7] IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy
[8] Istanbul Univ, Dept Neurol, Neuromuscular Unit, Istanbul Fac Med, Istanbul, Turkey
[9] Heidelberg Univ Hosp, Heidelberg, Germany
[10] Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden
[11] Ionis Pharmaceut Inc, Carlsbad, CA USA
[12] Ctr Hosp Univ Porto, Porto, Portugal
来源：
JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM | 2022年 / 27卷
关键词：
amyloidosis; transthyretin; eplontersen; clinical trial; patient characteristics;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：S144 / S144
页数：1
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