First conditional marketing authorization approval in the European Union for hemophilia "A" gene therapy

被引：18

作者：

VandenDriessche, Thierry ^{[1
,2
]}

Pipe, Steven W. ^{[3
,4
]}

Pierce, Glenn F. ^{[5
]}

Kaczmarek, Radoslaw ^{[6
]}

机构：

[1] Vrije Univ Brussel, Dept Gene Therapy & Regenerat Med, Brussels, Belgium

[2] Univ Leuven, Ctr Mol & Vasc Biol, Dept Cardiovasc Sci, Leuven, Belgium

[3] Univ Michigan, Dept Pediat, Ann Arbor, MI USA

[4] Univ Michigan, Dept Pathol, Ann Arbor, MI USA

[5] World Federat Hemophilia, Montreal, PQ, Canada

[6] Indiana Univ Sch Med, Dept Pediat, Indianapolis, IN 46202 USA

来源：

MOLECULAR THERAPY | 2022年 / 30卷 / 11期

基金：

欧盟地平线“2020”;

关键词：

D O I：

10.1016/j.ymthe.2022.09.020

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：3335 / 3336

页数：2

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