Preservation of function over time as measured by North Star ambulatory assessment in boys with nonsense mutation Duchenne muscular dystrophy treated with ataluren

被引：0
|
作者：
McDonald, C. [1 ]
Wei, L. [2 ]
Jin, F. [3 ]
Elfring, G. [3 ]
Trifillis, P. [3 ]
Souza, M. [3 ]
McIntosh, J. [3 ]
Peltz, S. [3 ]
Muntoni, F. [4 ]
机构：
[1] Univ Calif Davis, Sacramento, CA 95817 USA
[2] Harvard Univ, Boston, MA 02115 USA
[3] PTC Therapeut Inc, South Plainfield, NJ USA
[4] UCL, London, England
来源：
NEUROMUSCULAR DISORDERS | 2018年 / 28卷
关键词：
D O I：
10.1016/j.nmd.2018.06.139
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P.111
引用
收藏
页码：S62 / S63
页数：2
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