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- [1] Sirolimus for progressive neurofibromatosis type 1-associated plexiform neurofibromas: a Neurofibromatosis Clinical Trials Consortium phase II studyNEURO-ONCOLOGY, 2015, 17 (04) : 596 - 603Weiss, Brian论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USAWidemann, Brigitte C.论文数: 0 引用数: 0 h-index: 0机构: NCI, Pediat Oncol Branch, Bethesda, MD 20892 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USAWolters, Pamela论文数: 0 引用数: 0 h-index: 0机构: NCI, Pediat Oncol Branch, Bethesda, MD 20892 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USADombi, Eva论文数: 0 引用数: 0 h-index: 0机构: NCI, Pediat Oncol Branch, Bethesda, MD 20892 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USAVinks, Alexander论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Clin Pharmacol, Cincinnati, OH 45229 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USACantor, Alan论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Dept Prevent Med, Birmingham, AL USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USAPerentesis, John论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USASchorry, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Genet, Cincinnati, OH 45229 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USAUllrich, Nicole论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dept Neurol, Boston, MA USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USAGutmann, David H.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Neurol, St Louis, MO USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USATonsgard, James论文数: 0 引用数: 0 h-index: 0机构: Univ Chicago Med, Comer Childrens Hosp, Div Neurol, Chicago, IL USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USAViskochil, David论文数: 0 引用数: 0 h-index: 0机构: Primary Childrens Med Ctr, Div Genet, Salt Lake City, UT USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USA论文数: 引用数: h-index:机构:Packer, Roger J.论文数: 0 引用数: 0 h-index: 0机构: Ctr Neurosci & Behav Med, Childrens Natl Hlth Syst, Washington, DC USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USAFisher, Michael J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Oncol, Philadelphia, PA 19104 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Canc & Blood Dis Inst, Cincinnati, OH 45229 USA
- [2] A phase II study of continuous oral mTOR inhibitor everolimus for recurrent, radiographic-progressive neurofibromatosis type 1-associated pediatric low-grade glioma: a Neurofibromatosis Clinical Trials Consortium studyNEURO-ONCOLOGY, 2020, 22 (10) : 1527 - 1535Ullrich, Nicole J.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USA Dana Farber Canc Inst, Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA 02115 USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAPrabhu, Sanjay P.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dept Radiol, Boston, MA 02115 USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAReddy, Alyssa T.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Sch Med, Dept Neurol, San Francisco, CA USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAFisher, Michael J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Oncol, Philadelphia, PA 19104 USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAPacker, Roger论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl Hlth Syst, Ctr Neurosci & Behav Med, Washington, DC USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAGoldman, Stewart论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert Lurie Childrens Hosp, Chicago, IL USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USARobison, Nathan J.论文数: 0 引用数: 0 h-index: 0机构: Univ Southern Calif, Childrens Ctr Canc & Blood Dis, Childrens Hosp Los Angeles, Keck Sch Med, Los Angeles, CA 90007 USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAGutmann, David H.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAViskochil, David H.论文数: 0 引用数: 0 h-index: 0机构: Univ Utah, Dept Genet, Salt Lake City, UT USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAAllen, Jeffrey C.论文数: 0 引用数: 0 h-index: 0机构: NYU Langone Med Ctr, NYU Canc Inst, Dept Pediat, New York, NY USA NYU Langone Med Ctr, NYU Canc Inst, Dept Neurol, New York, NY USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USA论文数: 引用数: h-index:机构:Cantor, Alan论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Dept Preventat Med, Birmingham, AL USA Univ Cincinnati, Coll Med, Dept Pediat, Cincinnati, OH USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USACutter, Gary论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Sch Publ Hlth, Birmingham, AL 35294 USA Univ Cincinnati, Coll Med, Dept Pediat, Cincinnati, OH USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAThomas, Coretta论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Sch Publ Hlth, Birmingham, AL 35294 USA Univ Cincinnati, Coll Med, Dept Pediat, Cincinnati, OH USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAPerentesis, John P.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USA Univ Cincinnati, Coll Med, Dept Pediat, Cincinnati, OH USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAMizuno, Tomoyuki论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Clin Pharmacol, Cincinnati, OH 45229 USA Univ Cincinnati, Coll Med, Dept Pediat, Cincinnati, OH USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAVinks, Alexander A.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Clin Pharmacol, Cincinnati, OH 45229 USA Univ Cincinnati, Coll Med, Dept Pediat, Cincinnati, OH USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAManley, Peter E.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dept Hematol Oncol, Boston, MA 02115 USA Dana Farber Canc Inst, Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA 02115 USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAChi, Susan N.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dept Hematol Oncol, Boston, MA 02115 USA Dana Farber Canc Inst, Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA 02115 USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USAKieran, Mark W.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dept Hematol Oncol, Boston, MA 02115 USA Dana Farber Canc Inst, Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA 02115 USA Boston Childrens Hosp, Dept Neurol, 300 Longwood Ave, Boston, MA 02115 USA
- [3] TOLERABILITY OF THE MTOR INHIBITOR SIROLIMUS IN A PHASE II STUDY FOR NEUROFIBROMATOSIS TYPE 1 (NF1)-ASSOCIATED PLEXIFORM NEUROFIBROMAS: A NEUROFIBROMATOSIS CONSORTIUM STUDYNEURO-ONCOLOGY, 2010, 12 (06) : II85 - II85Weiss, B.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAWidemann, B. C.论文数: 0 引用数: 0 h-index: 0机构: NIH, Bethesda, MD 20892 USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USACantor, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama, Sch Med, Birmingham, AL USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAPerentesis, J.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAVinks, A.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAUllrich, N.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Boston, Boston, MA USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAGutmann, D.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, St Louis, MO USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAKorp, B.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama, Sch Med, Birmingham, AL USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAPacker, R.论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl Med Ctr, Washington, DC 20010 USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAFisher, M. J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USA
- [4] PHASE 2 STUDY OF THE MTOR INHIBITOR SIROLIMUS FOR PROGRESSIVE NF1-ASSOCIATED PLEXIFORM NEUROFIBROMAS (PN): A NEUROFIBROMATOSIS CLINICAL TRIALS CONSORTIUM STUDYNEURO-ONCOLOGY, 2014, 16 : 129 - 129Fisher, Michael J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAWidemann, Brigitte C.论文数: 0 引用数: 0 h-index: 0机构: NCI, Pediat Oncol Branch, Bethesda, MD 20892 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USADombi, Eva论文数: 0 引用数: 0 h-index: 0机构: NCI, Pediat Oncol Branch, Bethesda, MD 20892 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAWolters, Pamela论文数: 0 引用数: 0 h-index: 0机构: NCI, Pediat Oncol Branch, Bethesda, MD 20892 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USACantor, Alan论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Birmingham, AL USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAVinks, Alexander论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Cincinnati, OH 45229 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAParentesis, John论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Cincinnati, OH 45229 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAUllrich, Nicole论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp, Boston, MA 02115 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA论文数: 引用数: h-index:机构:Viskochil, David论文数: 0 引用数: 0 h-index: 0机构: Primary Childrens Med Ctr, Salt Lake City, UT USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USATonsgard, James论文数: 0 引用数: 0 h-index: 0机构: Univ Chicago, Chicago, IL 60637 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA论文数: 引用数: h-index:机构:Packer, Roger论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl Med Ctr, Washington, DC 20010 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USAWeiss, Brian论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Cincinnati, OH 45229 USA Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
- [5] PHASE II STUDY OF THE MTOR INHIBITOR SIROLIMUS FOR NON-PROGRESSIVE NF1-ASSOCIATED PLEXIFORM NEUROFIBROMAS: A NEUROFIBROMATOSIS CONSORTIUM STUDYNEURO-ONCOLOGY, 2010, 12 (06) : II43 - II43Weiss, B.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAFisher, M. J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USADombi, E.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Bethesda, MD USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USACantor, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama, Med Sch Birmingham, Birmingham, AL USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAVinks, A.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAKorf, B.论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama, Med Sch Birmingham, Birmingham, AL USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USASchorry, E.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAGutmann, D.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, St Louis, MO USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAPacker, R.论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl Med Ctr, Washington, DC 20010 USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USAWidemann, B. C.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Hlth, Bethesda, MD USA Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USA
- [6] Phase II study of the mTOR inhibitor sirolimus for nonprogressive NF1-associated plexiform neurofibromas: A Neurofibromatosis Consortium study.JOURNAL OF CLINICAL ONCOLOGY, 2010, 28 (15)Widemann, B. C.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USAFisher, M. J.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USADombi, E.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USACantor, A.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USAVinks, S.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USAKorf, B.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USASchorry, E.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USAGutmann, D.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USAPacker, R.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USAWeiss, B. D.论文数: 0 引用数: 0 h-index: 0机构: NCI, Bethesda, MD 20892 USA
- [7] MEK INHIBITOR BINIMETINIB SHOWS CLINICAL ACTIVITY IN CHILDREN WITH NEUROFIBROMATOSIS TYPE 1-ASSOCIATED PLEXIFORM NEUROFIBROMAS: A REPORT FROM PNOC AND THE NF CLINICAL TRIALS CONSORTIUMNEURO-ONCOLOGY, 2020, 22 : 420 - 421Mueller, Sabine论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, San Francisco, CA 94143 USA Childrens Hosp Zurich, Zurich, Switzerland Univ Calif San Francisco, San Francisco, CA 94143 USAReddy, Alyssa T.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, San Francisco, CA 94143 USA Univ Calif San Francisco, San Francisco, CA 94143 USADombi, Eva论文数: 0 引用数: 0 h-index: 0机构: NCI, Ctr Canc Res, Bethesda, MD 20892 USA Univ Calif San Francisco, San Francisco, CA 94143 USAAllen, Jeffrey论文数: 0 引用数: 0 h-index: 0机构: NYU Langone Hlth, New York, NY USA Univ Calif San Francisco, San Francisco, CA 94143 USAPacker, Roger论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl, Washington, DC USA Univ Calif San Francisco, San Francisco, CA 94143 USAClapp, Wade论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ, Sch Med, Indianapolis, IN USA Univ Calif San Francisco, San Francisco, CA 94143 USAGoldman, Stewart论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA Univ Calif San Francisco, San Francisco, CA 94143 USASchorry, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens, Cincinnati, OH USA Univ Calif San Francisco, San Francisco, CA 94143 USATonsgard, James论文数: 0 引用数: 0 h-index: 0机构: Univ Chicago, Dept Pediat, Chicago, IL 60637 USA Univ Calif San Francisco, San Francisco, CA 94143 USABlakeley, Jaishri论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Baltimore, MD USA Univ Calif San Francisco, San Francisco, CA 94143 USAUllrich, Nicole J.论文数: 0 引用数: 0 h-index: 0机构: Dana Farber Harvard Canc Ctr, Boston, MA USA Univ Calif San Francisco, San Francisco, CA 94143 USAGross, Andrea论文数: 0 引用数: 0 h-index: 0机构: NCI, Ctr Canc Res, Bethesda, MD 20892 USA Univ Calif San Francisco, San Francisco, CA 94143 USAWalsh, Karin论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl, Washington, DC USA Univ Calif San Francisco, San Francisco, CA 94143 USAThomas, Coretta论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Sch Publ Hlth, Birmingham, AL 35294 USA Univ Calif San Francisco, San Francisco, CA 94143 USAEdwards, Lloyd论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Sch Publ Hlth, Birmingham, AL 35294 USA Univ Calif San Francisco, San Francisco, CA 94143 USAPrados, Michael论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, San Francisco, CA 94143 USA Univ Calif San Francisco, San Francisco, CA 94143 USAKorf, Bruce论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Sch Publ Hlth, Birmingham, AL 35294 USA Univ Calif San Francisco, San Francisco, CA 94143 USAFisher, Michael J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Univ Calif San Francisco, San Francisco, CA 94143 USA
- [8] Treatment of neurofibromatosis type 1 (NF1)-related plexiform neurofibromas PN) with cabozantinib (XL184): A Neurofibromatosis Clinical Trials Consortium Phase II trialCANCER RESEARCH, 2019, 79 (13)Shih, Chie-Schin论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USABlakeley, Jaishri论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Med Ctr, Baltimore, MD USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAClapp, D. Wade论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAArmstrong, Amy E.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAWolters, Pam论文数: 0 引用数: 0 h-index: 0机构: NCI, Pediat Oncol Branch, Bethesda, MD 20892 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USADombi, Eva论文数: 0 引用数: 0 h-index: 0机构: NCI, Pediat Oncol Branch, Bethesda, MD 20892 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USACutter, Gary论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Birmingham, AL USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAUllrich, Nicole J.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAAllen, Jeffrey论文数: 0 引用数: 0 h-index: 0机构: NYU, New York, NY USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAPacker, Roger论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl Med Ctr, Washington, DC 20010 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAGoldman, Stewart论文数: 0 引用数: 0 h-index: 0机构: Lurie Childrens Hosp, Chicago, IL USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAGutmann, David H.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, St Louis, MO 63110 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAPlotkin, Scott论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Boston, MA 02114 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USARosser, Tena论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Los Angeles, CA 90027 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USARobertson, Kent论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAWidemann, Brigitte论文数: 0 引用数: 0 h-index: 0机构: NCI, Pediat Oncol Branch, Bethesda, MD 20892 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USARhodes, Steven论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAAngus, Steven论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC 27515 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USAJohnson, Gary论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Chapel Hill, NC 27515 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USA论文数: 引用数: h-index:机构:Fisher, Michael J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Indiana Univ, Riley Hosp Children, Indianapolis, IN 46204 USA
- [9] Sirolimus for Non-Progressive NF1-Associated Plexiform Neurofibromas: An NF Clinical Trials Consortium Phase II StudyPEDIATRIC BLOOD & CANCER, 2014, 61 (06) : 982 - 986Weiss, Brian论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USAWidemann, Brigitte C.论文数: 0 引用数: 0 h-index: 0机构: NCI, Dept Pediat Oncol, Bethesda, MD 20892 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USAWolters, Pamela论文数: 0 引用数: 0 h-index: 0机构: NCI, Dept Pediat Oncol, Bethesda, MD 20892 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USADombi, Eva论文数: 0 引用数: 0 h-index: 0机构: NCI, Dept Pediat Oncol, Bethesda, MD 20892 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USAVinks, Alexander A.论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Dept Pediat, Cincinnati, OH 45229 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USACantor, Alan论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama Birmingham, Dept Genet, Birmingham, AL USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USA论文数: 引用数: h-index:机构:Perentesis, John论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USAGutmann, David H.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Neurol, St Louis, MO USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USASchorry, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Dept Genet, Cincinnati, OH 45229 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USAPacker, Roger论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl Med Ctr, Washington, DC 20010 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USAFisher, Michael J.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Div Oncol, Philadelphia, PA 19104 USA Cincinnati Childrens Hosp Med Ctr, Div Oncol, Cincinnati, OH 45229 USA
- [10] Multicenter, phase 2 study of bevacizumab in children and adults with neurofibromatosis 2 and progressive vestibular schwannomas: an NF Clinical Trials Consortium studyNEUROLOGY, 2018, 90Plotkin, Scott论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USATonsgard, James论文数: 0 引用数: 0 h-index: 0机构: Univ Chicago, Chicago, IL 60637 USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USAUllrich, Nicole论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USAAllen, Jeffrey论文数: 0 引用数: 0 h-index: 0机构: NYU, Langone Med Ctr, New York, NY USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USABlakeley, Jaishri论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins, Baltimore, MD USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USARosser, Tena论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Los Angeles, Los Angeles, CA 90027 USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USAClapp, David论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ, Indianapolis, IN 46204 USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USACampion, Jian论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, St Louis, Ukraine Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USAFisher, Michael论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USACutter, Gary论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama, Birmingham, AL USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USA论文数: 引用数: h-index:机构:Packer, Roger论文数: 0 引用数: 0 h-index: 0机构: Childrens Natl Med Ctr, Neurol Dept, Washington, DC 20010 USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USAThomas, Coretta论文数: 0 引用数: 0 h-index: 0机构: Univ Alabama, Birmingham, AL USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USAKarajannis, Matthias论文数: 0 引用数: 0 h-index: 0机构: Mem Sloan Kettering Canc Ctr, 1275 York Ave, New York, NY 10021 USA Massachusetts Gen Hosp, Neurol, Boston, MA 02114 USA