Genetic therapies for spinal muscular atrophy type 1

被引：4
|
作者：
Aartsma-Rus, Annemieke [1 ]
机构：
[1] Leiden Univ, Med Ctr, Dept Human Genet, Albinusdreef 2, NL-2333 ZA Leiden, Netherlands
来源：
LANCET NEUROLOGY | 2018年 / 17卷 / 02期
基金：
欧盟第七框架计划;
关键词：
NUSINERSEN;
D O I：
10.1016/S1474-4422(17)30436-2
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：111 / 112
页数：3
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