Efficacy Evaluation of Liver-Directed Gene Theraphy in Fabry Mice

被引：4
|
作者：
Kia, Azadeh [1 ]
McIntosh, Jenny [2 ]
Rosales, Cecilia [2 ]
Hosseini, Paniz [1 ]
Sheridan, Rose [1 ]
Spiewak, Justyna [3 ]
Mills, Kevin [3 ]
Corbau, Romuald [1 ]
Nathwani, Amit C. [2 ,4 ,5 ]
机构：
[1] Freeline, Stevenage, Herts, England
[2] UCL, Inst Canc, Dept Haematol, London, England
[3] UCL Translat Mass Spectrometry, Ctr Inborn Errors Metab, London, England
[4] Royal Free NHS Fdn Trust, Katharine Dormandy Haemophilia Ctr, London, England
[5] Royal Free NHS Fdn Trust, Thrombosis Unit, London, England
来源：
BLOOD | 2018年 / 132卷
关键词：
D O I：
10.1182/blood-2018-99-116632
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
2209
引用
收藏
页数：2
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