Tongue and Hypoglossal Motoneuron Gene Therapy in a Rat Model of Pompe Disease

被引：1
|
作者：
Singer, Michele
Rana, Sabhya
Pope, Megan
Patterson, LiAna
Corti, Manuela
Byrne, Barry
Fuller, David
机构：
来源：
FASEB JOURNAL | 2021年 / 35卷
关键词：
D O I：
10.1096/fasebj.2021.35.S1.02822
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
引用
收藏
页数：2
相关论文
共 50 条
  • [21] Liver depot gene therapy for Pompe disease
    Kishnani, Priya S.
    Koeberl, Dwight D.
    ANNALS OF TRANSLATIONAL MEDICINE, 2019, 7 (13)
  • [22] Current avenues of gene therapy in Pompe disease
    Leon-Astudillo, Carmen
    Trivedi, Prasad D.
    Sun, Ramon C.
    Gentry, Matthew S.
    Fuller, David D.
    Byrne, Barry J.
    Corti, Manuela
    CURRENT OPINION IN NEUROLOGY, 2023, 36 (05) : 464 - 473
  • [23] Functional anatomy of the hypoglossal innervated muscles of the rat tongue: A model for elongation and protrusion of the mammalian tongue
    McClung, JR
    Goldberg, SJ
    ANATOMICAL RECORD, 2000, 260 (04): : 378 - 386
  • [24] AAV Therapy Attenuates Respiratory Dysfunction in a Novel Rat Model of Pompe Disease
    Mahajan, Bhuvna
    Vaught, Lauren A.
    Todd, A. Gary
    Duncanson, Lauren A.
    Doyle, Brendan
    Fuller, David D.
    Byrne, Barry J.
    Falk, Darin J.
    MOLECULAR THERAPY, 2018, 26 (05) : 166 - 166
  • [25] Opiate-Induced Suppression of Rat Hypoglossal Motoneuron Activity and Its Reversal by Ampakine Therapy
    Lorier, Amanda R.
    Funk, Gregory D.
    Greer, John J.
    PLOS ONE, 2010, 5 (01):
  • [26] Reduction of Autophagic Accumulation in Pompe Disease Mouse Model Following Gene Therapy
    McCall, Angela L.
    Stankov, Sylvia G.
    Cowen, Gabrielle
    Cloutier, Denise
    Zhang, Zizhao
    Yang, Lin
    Clement, Nathalie
    Falk, Darin J.
    Byrne, Barry J.
    CURRENT GENE THERAPY, 2019, 19 (03) : 197 - 207
  • [27] Bright tongue sign in Pompe disease
    Karam, Chafic
    NEUROLOGY, 2016, 86 (04) : 401 - 401
  • [28] AAV-GAA Gene Therapy Clears Long Chain Length Neuronal Glycogen in a Pompe Disease Rat Model
    Fuller, David D.
    Rana, Sabhya
    Ribas, Roberto A.
    Shedlock, Cameron J.
    Larson, Reece
    PHYSIOLOGY, 2024, 39
  • [29] POSTNATAL CHANGES IN RAT HYPOGLOSSAL MOTONEURON MEMBRANE-PROPERTIES
    VIANA, F
    BAYLISS, DA
    BERGER, AJ
    NEUROSCIENCE, 1994, 59 (01) : 131 - 148
  • [30] Immunomodulatory, liver depot gene therapy for Pompe disease
    Bond, J. E.
    Kishnani, P. S.
    Koeberl, D. D.
    CELLULAR IMMUNOLOGY, 2019, 342
12345