Development of a standard of care for patients with valosin-containing protein associated multisystem proteinopathy

被引：0

作者：

Korb, M. ^{[1
]}

Peck, A. ^{[2
]}

Berger, K. ^{[3
]}

James, M. ^{[4
]}

Ghoshal, N. ^{[5
]}

Healzer, E. ^{[6
]}

Henchcliffe, C. ^{[1
]}

Khan, S. ^{[7
]}

Mammen, P. ^{[7
]}

Patel, S. ^{[8
]}

Pfeffer, G. ^{[9
]}

Ralston, S. ^{[10
]}

Roy, B. ^{[11
]}

Seeley, B. ^{[12
]}

Swenson, A. ^{[13
]}

Mozaffar, T. ^{[1
]}

Weihl, C. ^{[5
]}

Kimonis, V. ^{[1
]}

Alfano, L. ^{[14
]}

机构：

[1] UC Irvine Sch Med, Orange, CA USA

[2] Cure VCP Dis, Americus, GA USA

[3] NYU, Grossman Sch Med, New York, NY USA

[4] John Walton Muscular Dystrophy Res Ctr, Newcastle Upon Tyne, Tyne & Wear, England

[5] Washington Univ, St Louis, MO 63110 USA

[6] Thriving Hope Consulting, Vinton, VA USA

[7] UT Southwestern Sch Med, Dallas, TX USA

[8] Wellness Sujata, Wadsworth, OH USA

[9] Univ Calgary, Cumming Sch Med, Calgary, AB, Canada

[10] Univ Edinburgh, Edinburgh, Midlothian, Scotland

[11] Yale Sch Med, New Haven, CT USA

[12] Univ Calif San Francisco, San Francisco, CA 94143 USA

[13] Univ Iowa Hosp & Clin, Iowa City, IA 52242 USA

[14] Nationwide Childrens Hosp, Columbus, OH USA

来源：

NEUROMUSCULAR DISORDERS | 2021年 / 31卷

关键词：

D O I：

10.1016/j.nmd.2021.07.372

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

EP.347

引用

页码：S155 / S156

页数：2

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