Chaperone therapy for mucopolysaccharidosis type IIIC

被引：1
|
作者：
Pshezhetsky, Alexey V. [1 ]
Pan, Xuefang [1 ]
Heon-Roberts, Rachel [1 ]
Li, Shao-Gang [2 ]
Wu, Harry Y. [1 ]
Taherzadeh, Mahsa [1 ]
De Aragao, Camila De Britto Para [1 ]
Wood, Jill [3 ]
Ekins, Sean [3 ]
Boyd, Robert [3 ]
Freundlich, Joel S. [2 ]
机构：
[1] Univ Montreal, CHU Ste Justine, Montreal, PQ, Canada
[2] Rutgers State Univ, New Jersey Med Sch, Newark, NJ USA
[3] Phoenix Nest Inc, New York, NY USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2018年 / 123卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2017.12.329
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
320
引用
收藏
页码：S121 / S122
页数：2
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