Correction of a mouse model of sickle cell disease:: Lentiviral/anti-sickling β-globin gene transduction of unmobilized, purified hematopoietic stem cells.
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作者:
Levasseur, DN
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Univ Alabama, Birmingham, AL USAUniv Alabama, Birmingham, AL USA
Levasseur, DN
[1
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Ryan, TM
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Univ Alabama, Birmingham, AL USAUniv Alabama, Birmingham, AL USA
Ryan, TM
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Pawlik, KM
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Univ Alabama, Birmingham, AL USAUniv Alabama, Birmingham, AL USA
Pawlik, KM
[1
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Townes, TM
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Univ Alabama, Birmingham, AL USAUniv Alabama, Birmingham, AL USA
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Genethon, Evry, France
Harvard Med Sch, Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA USAGenethon, Evry, France
Poletti, Valentina
Urbinati, Fabrizia
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Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USAGenethon, Evry, France
Urbinati, Fabrizia
Charrier, Sabine
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Genethon, Evry, FranceGenethon, Evry, France
Charrier, Sabine
Corre, Guillaume
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Genethon, Evry, FranceGenethon, Evry, France
Corre, Guillaume
Hollis, Roger P.
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Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USAGenethon, Evry, France
Hollis, Roger P.
Fernandez, Beatriz Campo
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Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USAGenethon, Evry, France
Fernandez, Beatriz Campo
Martin, Samia
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Genethon, Evry, FranceGenethon, Evry, France
Martin, Samia
Rothe, Michael
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Hannover Med Sch, Inst Expt Hematol, Hannover, GermanyGenethon, Evry, France
Rothe, Michael
Schambach, Axel
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Hannover Med Sch, Inst Expt Hematol, Hannover, Germany
Harvard Med Sch, Boston Childrens Hosp, Div Hematol Oncol, Boston, MA USAGenethon, Evry, France
Schambach, Axel
Kohn, Donald B.
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Univ Calif Los Angeles, Dept Microbiol Immunol & Mol Genet, Los Angeles, CA USAGenethon, Evry, France
Kohn, Donald B.
Mavilio, Fulvio
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Univ Modena & Reggio Emilia, Dept Life Sci, Via Campi 287, I-41125 Modena, Italy
Paris Descartes Univ, Imagine Inst, Paris, FranceGenethon, Evry, France
机构:
Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAUniv Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA
Morgan, Richard A.
Unti, Mildred
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Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAUniv Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA
Unti, Mildred
Hollis, Roger P.
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Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAUniv Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA
Hollis, Roger P.
Kohn, Donald B.
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Univ Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USAUniv Calif Los Angeles, Microbiol Immunol & Mol Genet, Los Angeles, CA USA