The Primary Immune Deficiency Treatment Consortium: how can it improve definitive therapy for PID?

被引:2
|
作者
Cowan, Morton J. [1 ]
机构
[1] UCSF Dept Pediat, Allergy Immunol & Blood & Marrow Transplant Div, San Francisco, CA 94143 USA
关键词
Primary immune deficiency; SCID; Wiskott Aldrich syndrome; chronic granulomatous disease; hematopoietic cell transplantation; gene therapy; enzyme replacement therapy; SEVERE COMBINED IMMUNODEFICIENCY; HEMATOPOIETIC-CELL TRANSPLANTATION; OUTCOMES; CHILDREN;
D O I
10.1080/1744666X.2016.1216317
中图分类号
R392 [医学免疫学]; Q939.91 [免疫学];
学科分类号
100102 ;
摘要
引用
收藏
页码:1007 / 1009
页数:3
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