Intravenous Lentiviral Gene Therapy for Hemophilia a: In Vitro and In Vivo Assessment of Universal Versus Tissue-Specific Promoters

被引：0
|
作者：
Gong, Jie [1 ]
Chung, Tsai-Hua [1 ,2 ]
Zhou, Min [3 ]
Chang, Lung-Ji [1 ,2 ]
机构：
[1] Univ Elect Sci & Technol China, Sch Med, Chengdu, Peoples R China
[2] Geno Immune Med Inst, Shenzhen, Peoples R China
[3] Univ Elect Sci & Technol China, Chengdu Womens & Childrens Cent Hosp, Sch Med, Chengdu, Peoples R China
来源：
BLOOD | 2021年 / 138卷
关键词：
D O I：
10.1182/blood-2021-147686
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：3
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