Novel riboswitches regulate AAV delivered transgene expression in mammals via small molecule inducers

被引：0
|
作者：
Forbes, A. J. [1 ]
Guo, X. [1 ]
Feng, L. [1 ]
Zhong, Z. [1 ]
Zhang, H. [1 ]
Saengtawesin, W. [1 ]
Taruc, P. [1 ]
Zeller, M. J. [2 ]
Li, K. [3 ]
Aube, J. [3 ]
Weeks, K. [2 ]
Waksal, S. D. [1 ]
机构：
[1] MeiraGTx, Gene Regulat, New York, NY 10016 USA
[2] Univ N Carolina, Dept Chem, Chapel Hill, NC 27599 USA
[3] Univ N Carolina, UNC Eshelman Sch Pharm, Div Chem Biol & Med Chem, Chapel Hill, NC 27599 USA
来源：
HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P164
引用
收藏
页码：A79 / A79
页数：1
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