A preliminary analysis from the ICGG Gaucher registry: Short-term clinical outcomes in Gaucher patients affected by the shortage of imiglucerase

被引：0

作者：

Weinreb, Neal ^{[1
]}

Rosenbloom, Barry ^{[2
]}

Andersson, Hans ^{[3
]}

Cole, Alexander ^{[4
]}

Tripuraneni, Radhika ^{[4
]}

Belmatoug, Nadia ^{[5
]}

机构：

[1] Univ Res Fdn Lysosomal Storage Disorders, Coral Springs, FL USA

[2] Tower Hematol Oncol, Beverly Hills, CA USA

[3] Tulane Univ, Med Ctr, New Orleans, LA USA

[4] Genzyme Corp, Cambridge, MA USA

[5] Hop Beaujon, Paris, France

来源：

MOLECULAR GENETICS AND METABOLISM | 2011年 / 102卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2010.11.153

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：S45 / S45

页数：1

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