Effect of different dosing regimens of exon skipping antisense oligonucleotides on functional outcome in the mdx mouse model of Duchenne muscular dystrophy

被引：0
|
作者：
Datson, N. [1 ]
Weij, R. [1 ]
Bijl, S. [1 ]
Janson, A. [1 ]
Vermue, R. [1 ]
Testerink, J. [1 ]
van Deutekom, J. [1 ]
机构：
[1] BioMarin, Leiden, Netherlands
来源：
NEUROMUSCULAR DISORDERS | 2015年 / 25卷
关键词：
D O I：
10.1016/j.nmd.2015.06.375
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
G.P.351
引用
收藏
页码：S291 / S291
页数：1
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