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- [1] New insights into AAV vectors integration profile: internal vector regionsHUMAN GENE THERAPY, 2015, 26 (10) : A3 - A3Gil-Farina, I.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, Germany Natl Ctr Tumor Dis NCT, Heidelberg, Germany DKFZ, Heidelberg, GermanyKaeppel, C.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, GermanyWilkening, S.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, GermanyRodriguez, M. A. Paneda论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, GermanyLopez-Franco, E.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, GermanyFontanellas, A.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, GermanyPrieto, J.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, GermanySpronck, L.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, Germanyvon Kalle, C.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, GermanyPetry, H.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, GermanyGonzalez-Aseguinolaza, G.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, GermanySchmidt, M.论文数: 0 引用数: 0 h-index: 0机构: DKFZ, Heidelberg, Germany
- [2] Molecular evaluation and vector integration analysis of HCC complicating AAV gene therapy for hemophilia BBLOOD ADVANCES, 2023, 7 (17) : 4966 - 4969Schmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: Genewerk GmbH, Heidelberg, Germany Genewerk GmbH, Heidelberg, GermanyFoster, Graham R.论文数: 0 引用数: 0 h-index: 0机构: Queen Mary Univ London, Barts Liver Ctr, London, England Genewerk GmbH, Heidelberg, GermanyCoppens, Michiel论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Amsterdam Univ Med Ctr, Amsterdam, Netherlands Amsterdam Cardiovasc Sci, Pulm Hypertens & Thrombosis, Amsterdam, Netherlands Genewerk GmbH, Heidelberg, GermanyThomsen, Hauke论文数: 0 引用数: 0 h-index: 0机构: Genewerk GmbH, Heidelberg, Germany Genewerk GmbH, Heidelberg, GermanyDolmetsch, Ricardo论文数: 0 引用数: 0 h-index: 0机构: UniQure Inc, Lexington, MA USA Genewerk GmbH, Heidelberg, GermanyHeijink, Liesbeth论文数: 0 引用数: 0 h-index: 0机构: UniQure Biopharm BV, Amsterdam, Netherlands Genewerk GmbH, Heidelberg, GermanyMonahan, Paul E.论文数: 0 引用数: 0 h-index: 0机构: CSL Behring, King Of Prussia, PA USA CSL Behring, 1020 1st Ave, King Of Prussia, PA 19406 USA Genewerk GmbH, Heidelberg, GermanyPipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pediat, Ann Arbor, MI USA Univ Michigan, Dept Pathol, Ann Arbor, MI USA Univ Michigan, Pediat & Pathol, 1500 E Med Ctr Dr, Ann Arbor, MI 48109 USA Genewerk GmbH, Heidelberg, Germany
- [3] ANALYSIS OF RETROVIRAL INTEGRATION SITES USING LAM-PCR TO SUPPORT THE INITIATION OF A PHASE I CANCER GENE THERAPY TRIALJOURNAL OF GENE MEDICINE, 2009, 11 (09): : 850 - 850Hyman, Jessica论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Westmead, Oncol Res Unit, Westmead, NSW, Australia Childrens Hosp Westmead, Oncol Res Unit, Westmead, NSW, AustraliaKramer, Belinda A.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Westmead, Oncol Res Unit, Westmead, NSW, Australia Childrens Hosp Westmead, Oncol Res Unit, Westmead, NSW, AustraliaGinn, Samantha L.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Westmead, Oncol Res Unit, Westmead, NSW, AustraliaAlexander, Ian E.论文数: 0 引用数: 0 h-index: 0机构: Univ Sydney, Discipline Paediat & Child Hlth, Sydney, NSW 2006, Australia Childrens Hosp Westmead, Oncol Res Unit, Westmead, NSW, Australia
- [4] Preclinical Safety Studies for AAV2-MerTK Gene Therapy Vector for Retinitis PigmentosaMOLECULAR THERAPY, 2013, 21 : S23 - S23Conlon, Thomas J.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USADeng, Wen-Tao论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USARyals, Renee C.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAErger, Kirsten E.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USACossette, Travis L.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USABoye, Shannon E.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAMcDoom, Isaam论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAClemente, Nathalie论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USACleaver, Brian论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAPotter, Mark论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAAbernathy, Corinne论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Clin & Translat Sci Inst, Gainesville, FL USA Univ Florida, Gainesville, FL USABoye, Sanford L.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USAHauswirth, William W.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Gainesville, FL USA Univ Florida, Gainesville, FL USA
- [5] A novel AAV design improving efficiency and safety in a gene therapy approach for Rett syndrome in a mouse modelHUMAN GENE THERAPY, 2018, 29 (12) : A79 - A80Giannelli, S. G.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyLuoni, M.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyMorabito, G.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyBido, S.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyIndrigo, M.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyNiro, A.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyRicci, R.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyValtorta, M.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyOrdazzo, G.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyRossi, G.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy Ist Sci San Raffaele, Milan, ItalyBroccoli, V.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy CNR Natl Res Council, Inst Neurosci, Via Vanvitelli 32, I-20129 Milan, Italy Ist Sci San Raffaele, Milan, Italy
- [6] Vector Analysis of Multicentric Lymphoma in a Severe Hemophilia. Dog after AAV Gene TherapyBLOOD, 2022, 140 : 4919 - 4920Van Gorder, Lucas论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USADoshi, Bhavya S.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USAWillis, Elinor论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USALanza, Matthew论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USAArruda, Valder R.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USACallan, Mary Beth论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Clin Sci & Adv Med, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USASamelson-Jones, Ben J.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA
- [7] The effect of exercise on improving strength and function in a Pompe mouse model treated with AAV vector mediated gene therapyMOLECULAR GENETICS AND METABOLISM, 2011, 102 (02) : S10 - S10论文数: 引用数: h-index:机构:Prater, Sean论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Durham, NC USA Duke Univ, Durham, NC USARodriguiz, Ramona论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Durham, NC USA Duke Univ, Durham, NC USA论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Koeberl, Dwight论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Durham, NC USA Duke Univ, Durham, NC USA
- [8] Safety and Toxicology of Ocular Gene Therapy with Recombinant AAV Vector rAAV.hCNGA3 in Nonhuman PrimatesHUMAN GENE THERAPY CLINICAL DEVELOPMENT, 2019, 30 (02) : 50 - 56Tobias, Peters论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Tubingen, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyPhilipp, Seitz Immanuel论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyStylianos, Michalakis论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilian Univ Munich, Ctr Integrated Prot Sci Munich, Dept Pharm, Ctr Drug Res, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyMartin, Biel论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilian Univ Munich, Ctr Integrated Prot Sci Munich, Dept Pharm, Ctr Drug Res, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBarbara, Wilhelm论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyFelix, Reichel论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyAlexander, Ochakovski Guy论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyEberhart, Zrenner论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Werner Reichardt Ctr Integrat Neurosci, Tubingen, Germany Univ Tubingen, Ctr Ophthalmol, Inst Ophthalm Res, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyMarius, Ueffing论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Inst Ophthalm Res, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBirgit, Korbmacher论文数: 0 引用数: 0 h-index: 0机构: Covance Preclin Serv GmbH, Munster, Germany Univ Eye Hosp Tubingen, Tubingen, GermanySven, Korte论文数: 0 引用数: 0 h-index: 0机构: Covance Preclin Serv GmbH, Munster, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyUlrich, Bartz-Schmidt Karl论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyDominik, Fischer Manuel论文数: 0 引用数: 0 h-index: 0机构: Univ Eye Hosp Tubingen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBartz-Schmidt, Karl Ulrich论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBolz, Sylvia论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyFischer, Dominik论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyKohl, Susanne论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyKuehlewein, Laura论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyMuehlfriedel, Regine论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyNeubauer, Jonas论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyOchakovski, Alex论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyPaquet-Durand, Francois论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanySeeliger, Mathias论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanySothilingam, Vithiyanjali论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyUeffing, Marius论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyWeisschuh, Nicole论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyWissinger, Bernd论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyZhour, Ahmad论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyZobor, Ditta论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyZrenner, Eberhart论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, Elfriede Aulhorn Str 7, D-72076 Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyBiel, Martin论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyMichalakis, Stylianos论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanySchoen, Christian论文数: 0 引用数: 0 h-index: 0机构: Ludwig Maximilians Univ Munchen, Ctr Drug Res, Dept Pharm, Munich, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyKahle, Nadine论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyPeters, Tobias论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyWilhelm, Barbara论文数: 0 引用数: 0 h-index: 0机构: Univ Tubingen, Ctr Ophthalmol, STZ Eyetrial, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, GermanyTsang, Steven论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Ophthalmol, New York, NY 10027 USA Univ Eye Hosp Tubingen, Tubingen, GermanyGloeckner, Christian Johannes论文数: 0 引用数: 0 h-index: 0机构: Deutsch Zentrum Neurodegenerat Erkrankungen, Tubingen, Germany Univ Eye Hosp Tubingen, Tubingen, Germany
- [9] Analysis of vector genome integrations in multicentric lymphoma after AAV gene therapy in a severe hemophilia A dogMOLECULAR THERAPY METHODS & CLINICAL DEVELOPMENT, 2023, 31Van Gorder, Lucas论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USADoshi, Bhavya S.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USAWillis, Elinor论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USANichols, Timothy C.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Dept Pathol & Lab Med, Chapel Hill, NC 27599 USA Univ N Carolina, UNC Blood Res Ctr, Chapel Hill, NC 27599 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USACook, Emma论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USAEverett, John K.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USAMerricks, Elizabeth P.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Dept Pathol & Lab Med, Chapel Hill, NC 27599 USA Univ N Carolina, UNC Blood Res Ctr, Chapel Hill, NC 27599 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USAArruda, Valder R.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USABushman, Frederic D.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Microbiol, Perelman Sch Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USACallan, Mary Beth论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Vet Med, Dept Clin Sci & Adv Med, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USASamelson-Jones, Benjamin J.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Pediat, Philadelphia, PA 19104 USA
- [10] ENHANCING EV-AAV INCORPORATION: INSIGHTS INTO NATURAL LOADING AND LOADING STRATEGIES FOR IMPROVED GENE THERAPY VECTOR DELIVERYCYTOTHERAPY, 2024, 26 (06) : S88 - S89Vorobieva, I.论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Paediat, Oxford, England Inst Dev & Regenerat Med, Oxford, Oxon, England Univ Oxford, Paediat, Oxford, EnglandFriedrichson, H.论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Paediat, Oxford, England Inst Dev & Regenerat Med, Oxford, Oxon, England Univ Oxford, Paediat, Oxford, EnglandAhlskog, N.论文数: 0 引用数: 0 h-index: 0机构: Inst Dev & Regenerat Med, Oxford, Oxon, England Univ Oxford, Paediat, Oxford, EnglandStaton, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Paediat, Oxford, England Inst Dev & Regenerat Med, Oxford, Oxon, England Univ Oxford, Paediat, Oxford, EnglandWood, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Oxford, Paediat, Oxford, England Inst Dev & Regenerat Med, Oxford, Oxon, England Muscular Dystrophy UK, London, England Univ Oxford, Paediat, Oxford, EnglandConceicao, M.论文数: 0 引用数: 0 h-index: 0机构: Inst Dev & Regenerat Med, Oxford, Oxon, England Evox Therapeut Ltd, Oxford, England Univ Oxford, Paediat, Oxford, England