Correction of Metabolic Abnormalities in Murine Glycogen Storage Disease Type Ib by Gene Therapy

被引:0
|
作者
Lee, Young Mok [1 ,2 ]
Kwon, Joonhyun [1 ]
Weinstein, David A. [2 ]
Chou, Janice Y. [1 ]
机构
[1] Eunice Kennedy Shriver Natl Inst Child Hlth & Hum, Sect Cellular Differentiat, Program Dev Endocrinol & Genet, NIH, Bethesda, MD USA
[2] Univ Florida, Dept Pediat, Div Pediat Endocrinol, Glycogen Storage Dis Program, Gainesville, FL USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
376
引用
收藏
页码:S150 / S150
页数:1
相关论文
共 50 条
  • [1] Prevention of Hepatocellular Adenoma and Correction of Metabolic Abnormalities in Murine Glycogen Storage Disease Type la by Gene Therapy
    Lee, Young Mok
    Jun, Hyun Sik
    Pan, Chi-Jiunn
    Lin, Su Ru
    Wilson, Lane H.
    Mansfield, Brian C.
    Chou, Janice Y.
    MOLECULAR THERAPY, 2012, 20 : S53 - S54
  • [2] Prevention of hepatocellular adenoma and correction of metabolic abnormalities in murine glycogen storage disease type Ia by gene therapy
    Lee, Young Mok
    Jun, Hyun Sik
    Pan, Chi-Jiunn
    Lin, Su Ru
    Wilson, Lane H.
    Mansfield, Brian C.
    Chou, Janice Y.
    HEPATOLOGY, 2012, 56 (05) : 1719 - 1729
  • [3] Sustained correction of Glycogen Storage Disease Type Ib mice by gene therapy
    Lee, Y. M.
    Estrella, A. M.
    Arends, C. J.
    HUMAN GENE THERAPY, 2021, 32 (19-20) : A102 - A102
  • [4] Liver-Directed Gene Therapy for Murine Glycogen Storage Disease Type IB
    Kwon, Joonhyun
    Cho, Jun-Ho
    Lee, Young Mok
    Kim, Goo-Young
    Anduaga, Javier
    Chou, Janice
    MOLECULAR THERAPY, 2016, 24 : S64 - S65
  • [5] Liver-directed gene therapy for murine glycogen storage disease type Ib
    Kwon, Joon Hyun
    Lee, Young Mok
    Cho, Jun-Ho
    Kim, Goo-Young
    Anduaga, Javier
    Starost, Matthew F.
    Mansfield, Brian C.
    Chou, Janice Y.
    HUMAN MOLECULAR GENETICS, 2017, 26 (22) : 4395 - 4405
  • [6] Molecular biology and gene therapy for glycogen storage disease type Ib
    Chou, Janice Y.
    Cho, Jun-Ho
    Kim, Goo-Young
    Mansfield, Brian C.
    JOURNAL OF INHERITED METABOLIC DISEASE, 2018, 41 (06) : 1007 - 1014
  • [7] Glucose-6-phosphate transporter gene therapy corrects metabolic and myeloid abnormalities in glycogen storage disease type Ib mice
    W H Yiu
    C-J Pan
    M Allamarvdasht
    S Y Kim
    J Y Chou
    Gene Therapy, 2007, 14 : 219 - 226
  • [8] Glucose-6-phosphate transporter gene therapy corrects metabolic and myeloid abnormalities in glycogen storage disease type Ib mice
    Yiu, W. H.
    Pan, C-J
    Allamarvdasht, M.
    Kim, S. Y.
    Chou, J. Y.
    GENE THERAPY, 2007, 14 (03) : 219 - 226
  • [9] Systemic Correction of Murine Glycogen Storage Disease Type IV by an AAV-Mediated Gene Therapy
    Yi, Haiqing
    Zhang, Quan
    Brooks, Elizabeth D.
    Yang, Chunyu
    Thurberg, Beth L.
    Kishnani, Priya S.
    Sun, Baodong
    HUMAN GENE THERAPY, 2017, 28 (03) : 286 - 294
  • [10] A case of glycogen storage disease type Ib presenting with prolonged neonatal hypoglycaemia and minimal metabolic abnormalities
    Matsumoto, Hiroshi
    Kajiwara, Shinsuke
    Ogura, Yumi
    Asano, Takako
    Horikawa, Reiko
    Nonoyama, Shigeaki
    ACTA PAEDIATRICA, 2010, 99 (02) : 163 - 164