The Adeno-Associated Viral Anc80 Vector Efficiently Transduces Hair Cells in Cynomolgus Macaques (M. Fascicularis): Development of a Non-Human Primate (NHP) Model for Cochlear Gene Therapy

被引：0
|
作者：
Francis, Shimon P. [1 ]
McKenna, Michael J. [2 ]
Ng, Robert [1 ]
Gao, Yuan [1 ]
Qu, Enping [1 ]
Vandenberghe, Luk H. [1 ]
Sewell, William J. [2 ]
Simons, Emmanuel J. [1 ]
Valero, Michelle D. [1 ]
机构：
[1] Akouos, Boston, MA USA
[2] Harvard Med Sch, Massachusetts Eye & Ear Infirm, Akouos, Boston, MA 02115 USA
来源：
MOLECULAR THERAPY | 2019年 / 27卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
234
引用
收藏
页码：116 / 117
页数：2
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