Induced Pluripotent Stem Cells as a Model To Test Gene Augmentation Therapy for Choroideremia

被引：0

作者：

Vasireddy, Vidyullatha ^{[1
]}

Mills, Jason A. ^{[2
]}

Gaddameedi, Rajashekhar ^{[1
]}

Basner-Tschakarjan, Etiena ^{[2
]}

Kohnke, Monica ^{[3
]}

Black, Aaron H. ^{[1
]}

Alexandrov, Krill ^{[3
]}

Maguire, Albert M. ^{[1
,2
]}

Chung, Daniel ^{[1
,2
]}

Mac, Helen ^{[2
]}

Sullivan, Lisa ^{[4
]}

Gadue, Paul ^{[2
,5
]}

Bennicelli, Jeannette L. ^{[1
]}

French, Deborah L. ^{[2
,5
]}

Bennett, Jean ^{[1
,2
]}

机构：

[1] Univ Penn, Schie Eye Inst, Philadelphia, PA 19104 USA

[2] Childrens Hosp Philadelphia, Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USA

[3] Univ Queensland, Inst Mol Biosci, St Lucia, Qld, Australia

[4] Children Hosp Philadelphia, Dept Anat Pathol, Philadelphia, PA USA

[5] Childrens Hosp Philadelphia, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA

来源：

MOLECULAR THERAPY | 2013年 / 21卷

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

224

引用

页码：S87 / S87

页数：1

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