DEVELOPMENT OF A DISEASE SEVERITY SCORING SYSTEM FOR TYPE 1 GAUCHER DISEASE

被引:0
|
作者
Zimran, A. [1 ]
Cappellini, M. D. [2 ]
Cox, T. [3 ]
Giannini, E. H. [4 ]
Grabowski, G. A. [4 ]
Hwu, W. L. [5 ]
Mankin, H. [6 ]
Martins, A. M. [7 ]
Sawyers, C. [8 ]
vom Dahl, S. [9 ]
Weinreb, N. [10 ]
Yeh, M. [8 ]
机构
[1] Shaare Zedek Med Ctr, Jerusalem, Israel
[2] Univ Milan, Policlin Fdn IRCCS, Milan, Italy
[3] Univ Cambridge, Cambridge, England
[4] Cincinnati Childrens Hosp, Med Ctr, Cincinnati, OH USA
[5] Natl Taiwan Univ Hosp, Taipei, Taiwan
[6] Massachusetts Gen Hosp, Boston, MA 02114 USA
[7] Univ Fed Sao Paulo, Sao Paulo, Brazil
[8] Genzyme Corp, Cambridge, MA USA
[9] St Franziskus Hosp, Cologne, Germany
[10] Univ Res Fdn Lysosomal Storage Disorders, Coral Springs, FL USA
关键词
D O I
暂无
中图分类号
R9 [药学];
学科分类号
1007 ;
摘要
引用
收藏
页码:S95 / S95
页数:1
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