Hematopoietic Stem Cell Gene Therapy with Lentiviral Vector in 4 Patients with Cerebral X-Linked Adrenoleukodystrophy

被引：0

作者：

Aubourg, Patrick ^{[1
,2
,3
]}

Hacein-Bey-Abina, Salima ^{[4
]}

Bartholomae, Cynthia ^{[5
]}

Schmidt, Manfred ^{[5
]}

Kutschera, Ina ^{[5
]}

Vidaud, Michel ^{[2
,3
]}

Dal-Cortivo, Liliane ^{[4
]}

Malhaoui, Nizar ^{[6
]}

Frange, Pierre ^{[6
]}

Bellesme, Celine ^{[1
]}

Lefrere, Francois ^{[4
]}

Dufayet, Gaelle ^{[2
,3
]}

Bougneres, Pierre ^{[7
]}

Fischer, Alain ^{[6
]}

von Kalle, Christof ^{[5
]}

Cavazzana-Calvo, Marina ^{[4
]}

Cartier, Nathalie ^{[1
,2
,3
]}

机构：

[1] Hop Bicetre, Dept Pediat Neurol, Le Kremlin Bicetre, France

[2] Univ Paris 05, Paris, France

[3] INSERM, UMR745, Paris, France

[4] Hop Necker Enfants Malad, Dept Biotherapy, Paris, France

[5] Natl Ctr Tumor Dis, German Canc Res Ctr DKFZ, Heidelberg, Germany

[6] Hop Necker Enfants Malad, Dept Pediat Immunohematol, Paris, France

[7] Hop Bicetre, Dept Pediat Endocrinol, Le Kremlin Bicetre, France

来源：

MOLECULAR THERAPY | 2012年 / 20卷

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

314

引用

页码：S124 / S124

页数：1

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[2] Hematopoietic Stem Cell Gene Therapy with Lentiviral Vector in X-linked Adrenoleukodystrophy
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