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- [2] A systematic review on effectiveness and safety of eliglustat for type 1 Gaucher disease[J]. EXPERT OPINION ON ORPHAN DRUGS, 2014, 2 (05): : 523 - 529Smid, Bouwien E.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Internal Med Endocrinol & Metab, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Internal Med Endocrinol & Metab, NL-1105 AZ Amsterdam, NetherlandsHollak, Carla E. M.论文数: 0 引用数: 0 h-index: 0机构: Univ Amsterdam, Acad Med Ctr, Dept Internal Med Endocrinol & Metab, NL-1105 AZ Amsterdam, Netherlands Univ Amsterdam, Acad Med Ctr, Dept Internal Med Endocrinol & Metab, NL-1105 AZ Amsterdam, Netherlands
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- [5] Recommendations for the use of eliglustat in the treatment of adults with Gaucher disease type 1 in the United States[J]. MOLECULAR GENETICS AND METABOLISM, 2016, 117 (02) : 95 - 103Balwani, Manisha论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, One Gustave L Levy Pl,Box 1497, New York, NY 10029 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, One Gustave L Levy Pl,Box 1497, New York, NY 10029 USABurrow, Thomas Andrew论文数: 0 引用数: 0 h-index: 0机构: Cincinnati Childrens Hosp Med Ctr, Div Human Genet, 3333 Burnet Ave,MLC 4006, Cincinnati, OH 45229 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, One Gustave L Levy Pl,Box 1497, New York, NY 10029 USACharrow, Joel论文数: 0 引用数: 0 h-index: 0机构: Northwestern Univ, Ann & Robert H Lurie Childrens Hosp Chicago, Div Genet Birth Defects & Metab, Dept Pediat,Feinberg Sch Med, 225 East Chicago Ave, Chicago, IL 60611 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, One Gustave L Levy Pl,Box 1497, New York, NY 10029 USAGoker-Alpan, Ozlem论文数: 0 引用数: 0 h-index: 0机构: O&O Alpan LLC, Lysosomal Disorders Unit, 11212 Waples Mill Rd, Fairfax, VA 22030 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, One Gustave L Levy Pl,Box 1497, New York, NY 10029 USAKaplan, Paige论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Lysosomal Ctr, Div Genet, Civ Ctr Blvd, Philadelphia, PA 19104 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, One Gustave L Levy Pl,Box 1497, New York, NY 10029 USAKishnani, Priya S.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Pediat, DUMC 103856,595 Lasalle St,GSRB 1,4th Floor, Durham, NC 27710 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, One Gustave L Levy Pl,Box 1497, New York, NY 10029 USA论文数: 引用数: h-index:机构:Ruskin, Jeremy论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp, Electrophysiol Lab, Arrhythmia Serv, 55 Fruit St, Boston, MA 02114 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, One Gustave L Levy Pl,Box 1497, New York, NY 10029 USAWeinreb, Neal论文数: 0 引用数: 0 h-index: 0机构: Univ Res Fdn Lysosomal Storage Dis Inc, 7367 Wexford Terrace, Boca Raton, FL 33433 USA Icahn Sch Med Mt Sinai, Dept Genet & Genom Sci, One Gustave L Levy Pl,Box 1497, New York, NY 10029 USA
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