Emicizumab prophylaxis and health-related outcomes in persons with hemophilia a (PwHA) with inhibitors: HAVEN 1 study

被引:0
|
作者
Oldenburg, J. [1 ]
Mahlangu, J. N. [2 ,3 ]
Bujan, W. [4 ]
Trask, P. C. [5 ]
von Mackensen, S. [6 ]
Callaghan, M. U. [7 ]
Young, G. [8 ]
Asikanius, E. [9 ]
Peyvandi, F. [10 ]
Santagostino, E. [10 ]
Kruse-Jarres, R. [11 ]
Negrier, C. [12 ]
Kessler, C. [13 ]
Levy, G. G. [14 ]
Windyga, J. [15 ]
Shima, M. [16 ]
机构
[1] Univ Klinikum Bonn, Bonn, Germany
[2] Univ Witwatersrand, Fac Hlth Sci, Haemophilia Comprehens Care Ctr, Johannesburg, South Africa
[3] NHLS, Johannesburg, South Africa
[4] Inst Costarricense Invest Cient, San Jose, Costa Rica
[5] Genentech Inc, San Francisco, CA 94080 USA
[6] Univ Med Ctr Hambur Eppendorf, Dept Med Psychol, Hamburg, Germany
[7] Childrens Hosp Michigan, Detroit Med Ctr, Detroit, MI 48201 USA
[8] Univ Southern Calif, Keck Sch Med, Childrens Hosp Los Angeles, Los Angeles, CA USA
[9] F Hoffmann La Roche Ltd, Basel, Switzerland
[10] Osped Maggiore Policlin, IRCCS Ca Granda Fdn, Milan, Italy
[11] Univ Washington, Washington Ctr Bleeding Disorders BloodWorks NW, Seattle, WA 98195 USA
[12] Univ Claude Bernard, Louis Pradel Cardiol Hosp, Lyon, France
[13] Georgetown Univ, Med Ctr, Washington, DC 20007 USA
[14] Genentech Inc, Pharma Dev Oncol, San Francisco, CA 94080 USA
[15] Inst Hematol & Transfus Med, Warsaw, Poland
[16] Nara Med Univ, Dept Pediat, Kashihara, Nara, Japan
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R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
P120
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页码:89 / 90
页数:2
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